Free tool

Rare disease stocks

We cover 31 companies grouped under the Rare disease theme. The median market value in the group is $10.53B. Across the group, the median move over the past trading day is −0.61%. 47% of the 30 with a 200-day average trade above it. Price change over the past year runs from −89.3% to +197.1% across the middle 80 percent of the group, with a median of 0.0%.

Other lists in this group

Table

31 of 268 companies match these filters.Clear filters

TickerCompanyMarket cap (USD)Size1Y returnNext report
VX1.DEVertex Pharmaceuticals Incorporated$139.82BLarge cap+41.64%Nov 2, 2026
VRTXVertex Pharmaceuticals Incorporated$138.63BLarge cap+40.66%Nov 2, 2026
DUL.DEAlnylam Pharmaceuticals, Inc.$32.28BLarge cap−10.21%Oct 29, 2026
ALNYAlnylam Pharmaceuticals, Inc.$32.12BLarge cap−47.38%Oct 29, 2026
INSMInsmed Incorporated$27.16BLarge cap−7.54%Oct 29, 2026
ROIVRoivant Sciences Ltd.$26.55BLarge cap+206.51%Nov 9, 2026
JAZZJazz Pharmaceuticals plc$16.89BLarge cap+100.35%Nov 4, 2026
BBIOBridgeBio Pharma, Inc.$15.52BLarge cap+60.05%Oct 28, 2026
CORTCorcept Therapeutics Incorporated$12.95BLarge cap+71.81%Nov 4, 2026
0JAV.LInsmed Incorporated$12.89BLarge cap−7.52%Oct 29, 2026
BMRNBioMarin Pharmaceutical Inc.$12.70BLarge cap+11.85%Oct 26, 2026
REC.MIRecordati Industria Chimica e Farmaceutica S.p.A.$12.57BLarge cap+1.80%Nov 10, 2026
ARWRArrowhead Pharmaceuticals, Inc.$12.52BLarge cap+308.99%Nov 24, 2026
CYTKCytokinetics, Incorporated$11.01BLarge cap+109.36%Nov 5, 2026
IONSIonis Pharmaceuticals, Inc.$10.56BLarge cap+48.21%Nov 4, 2026
KYMRKymera Therapeutics, Inc.$10.53BLarge cap+197.09%Nov 3, 2026
ABVX.PAABIVAX Société Anonyme$10.21BLarge cap+48.91%Sep 21, 2026
GOSSGossamer Bio, Inc.$85.01MMicro cap−92.93%Nov 4, 2026
SPROSpero Therapeutics, Inc.$71.05MMicro cap−38.38%Nov 12, 2026
SCYXSCYNEXIS, Inc.$56.41MMicro cap+579.04%Nov 4, 2026
ATYRaTyr Pharma, Inc.$54.05MMicro cap−89.34%Nov 5, 2026
MCRBSeres Therapeutics, Inc.$47.81MMicro cap−74.79%Nov 4, 2026
MREOMereo BioPharma Group plc$44.39MMicro cap−84.20%Nov 9, 2026
QNCXQuince Therapeutics, Inc.$31.84MMicro cap+100.71%Nov 12, 2026
RVX.TOResverlogix Corp.$24.81MMicro cap0.00%Nov 12, 2026
JSPRJasper Therapeutics, Inc.$23.96MMicro cap−75.24%Nov 10, 2026
TVRDTvardi Therapeutics, Inc.$23.74MMicro cap−94.18%Nov 12, 2026
INMInMed Pharmaceuticals Inc.$7.64MMicro cap−36.44%Sep 23, 2026
JAGXJaguar Health, Inc.$4.78MMicro cap−98.52%Nov 12, 2026
XRTXXORTX Therapeutics Inc.$4.03MMicro cap−43.99%Nov 12, 2026
APLI.TOAppili Therapeutics Inc.$1.44MMicro cap−25.00%Nov 12, 2026

Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.

More ways to browse