Rare disease stocks
Daily analysis · Oct 27, 2026
Today's data shows 82 companies rose, 80 fell and one was unchanged, while median one-year changes by size band ranged from +31.5% for mid caps to -51.5% for micro caps.
- Vertex Pharmaceuticals Incorporated (VRTX34.SA): +5.1% one day move, mega cap
- Alnylam Pharmaceuticals, Inc. (A1LN34.SA): +9.1% one day move, large cap
- Oruka Therapeutics, Inc. (ORKA): +12.7% one day move, mid cap
Generated from today's data · Not investment advice
Heavily traded in Rare disease
Turnover over $10M/day75 of about 230 companies in this theme turn over more than $10M in a typical session. Largest market value first. Data as of Oct 27, 2026.
| Company | Turnover | 1Y return | Next report |
|---|---|---|---|
| VRTXVertex Pharmaceuticals Incorporated | $494.46M | +23.16% | Reports Nov 2, 2026 |
| ARGXargenx SE | $241.59M | +4.76% | — |
| ALNYAlnylam Pharmaceuticals, Inc. | $325.24M | −52.43% | Reports Oct 29, 2026 |
| ROIVRoivant Sciences Ltd. | $222.91M | +91.65% | Reports Nov 9, 2026 |
| INSMInsmed Incorporated | $194.09M | −43.10% | Reports Oct 29, 2026 |
| ASNDAscendis Pharma A/S | $159.80M | +20.63% | — |
| JAZZJazz Pharmaceuticals plc | $149.80M | +47.64% | Reports Nov 2, 2026 |
| BBIOBridgeBio Pharma, Inc. | $169.79M | +7.22% | Reports Oct 29, 2026 |
Turnover is the median value traded in one session, measured over the past 50 sessions. It describes trading activity in a stock and nothing about the company behind it.
Table
227 companies, largest market value first.
Data as of Oct 27, 2026 · updates nightly, Mon–Sat
| Ticker | Company | Market cap (USD) | Size | 1Y return |
|---|---|---|---|---|
| VRTX | Vertex Pharmaceuticals Incorporated | $131.08B | Large cap | +23.16% |
| ARGX | argenx SE | $54.67B | Large cap | +4.76% |
| ALNY | Alnylam Pharmaceuticals, Inc. | $30.46B | Large cap | −52.43% |
| A1LN34.SA | Alnylam Pharmaceuticals, Inc. | $30.20B | Large cap | −52.23% |
| ROIV | Roivant Sciences Ltd. | $26.04B | Large cap | +91.65% |
| INSM | Insmed Incorporated | $20.38B | Large cap | −43.10% |
| ASND | Ascendis Pharma A/S | $16.13B | Large cap | +20.63% |
| JAZZ | Jazz Pharmaceuticals plc | $13.35B | Large cap | +47.64% |
| BBIO | BridgeBio Pharma, Inc. | $13.32B | Large cap | +7.22% |
| BMRN | BioMarin Pharmaceutical Inc. | $10.79B | Large cap | +5.85% |
| CORT | Corcept Therapeutics Incorporated | $9.42B | Mid cap | +20.07% |
| KYMR | Kymera Therapeutics, Inc. | $9.21B | Mid cap | +88.73% |
| PTGX | Protagonist Therapeutics, Inc. | $9.08B | Mid cap | +86.47% |
| CRNX | Crinetics Pharmaceuticals Inc | $9.01B | Mid cap | +91.59% |
| CYTK | Cytokinetics, Incorporated | $8.51B | Mid cap | +0.91% |
| ARWR | Arrowhead Pharmaceuticals, Inc. | $8.31B | Mid cap | +49.39% |
| 4151.T | Kyowa Kirin Co., Ltd. | $8.14B | Mid cap | +4.15% |
| IONS | Ionis Pharmaceuticals, Inc. | $7.22B | Mid cap | −40.51% |
| RYTM | Rhythm Pharmaceuticals, Inc. | $6.14B | Mid cap | −19.79% |
| IMVT | Immunovant, Inc. | $5.82B | Mid cap | +31.45% |
| MANE | Veradermics, Incorporated | $5.74B | Mid cap | +263.95% |
| KNSA | Kiniksa Pharmaceuticals International, plc | $5.61B | Mid cap | +79.75% |
| MIRM | Mirum Pharmaceuticals, Inc. | $5.41B | Mid cap | +16.33% |
| GRFS | Grifols, S.A. | $5.39B | Mid cap | −15.57% |
| ORKA | Oruka Therapeutics, Inc. | $5.31B | Mid cap | +226.10% |
| PTCT | PTC Therapeutics, Inc. | $5.10B | Mid cap | −8.96% |
| SRRK | Scholar Rock Holding Corporation | $5.08B | Mid cap | +36.75% |
| TVTX | Travere Therapeutics, Inc. | $4.65B | Mid cap | +67.85% |
| DNTH | Dianthus Therapeutics, Inc. | $4.34B | Mid cap | +136.66% |
| EWTX | Edgewise Therapeutics, Inc. | $4.25B | Mid cap | +144.35% |
| ARQT | Arcutis Biotherapeutics, Inc. | $4.00B | Mid cap | +61.97% |
| LQDA | Liquidia Corporation | $3.92B | Mid cap | +92.18% |
| IRON | Disc Medicine, Inc. | $3.45B | Mid cap | −13.37% |
| AMLX | Amylyx Pharmaceuticals, Inc. | $3.40B | Mid cap | +90.37% |
| DYN | Dyne Therapeutics, Inc. | $2.94B | Mid cap | −34.96% |
| VRDN | Viridian Therapeutics, Inc. | $2.64B | Mid cap | +3.55% |
| ADMA | ADMA Biologics, Inc. | $2.48B | Mid cap | −29.07% |
| CLDX | Celldex Therapeutics, Inc. | $2.32B | Mid cap | +7.78% |
| AUPH | Aurinia Pharmaceuticals Inc. | $2.27B | Mid cap | +38.65% |
| PHVS | Pharvaris N.V. | $2.21B | Mid cap | +38.21% |
| AGIO | Agios Pharmaceuticals, Inc. | $2.20B | Mid cap | −14.46% |
| VERA | Vera Therapeutics, Inc. | $2.02B | Mid cap | −6.94% |
| BCRX | BioCryst Pharmaceuticals, Inc. | $2.01B | Mid cap | +7.80% |
| SEPN | Septerna, Inc. | $1.89B | Small cap | +82.94% |
| XERS | Xeris Biopharma Holdings, Inc. | $1.86B | Small cap | +9.67% |
| MLYS | Mineralys Therapeutics, Inc. | $1.81B | Small cap | −49.31% |
| PVLA | Palvella Therapeutics, Inc. | $1.80B | Small cap | +79.23% |
| TRVI | Trevi Therapeutics, Inc. | $1.78B | Small cap | +19.14% |
| ZBIO | Zenas BioPharma, Inc. | $1.78B | Small cap | −14.34% |
| NEU.AX | Neuren Pharmaceuticals Limited | $1.75B | Small cap | −12.52% |
| MAZE | Maze Therapeutics, Inc. | $1.73B | Small cap | +0.23% |
| COAG | Hemab Therapeutics Holdings, Inc. | $1.68B | Small cap | +5.94% |
| ANIP | ANI Pharmaceuticals, Inc. | $1.67B | Small cap | −21.82% |
| STOK | Stoke Therapeutics, Inc. | $1.64B | Small cap | −22.85% |
| FBRX | Forte Biosciences Inc | $1.63B | Small cap | +492.23% |
| RARE | Ultragenyx Pharmaceutical Inc. | $1.59B | Small cap | −54.46% |
| TRAX | First Tracks Biotherapeutics, Inc. | $1.55B | Small cap | +128.84% |
| 009420.KS | Hanall Biopharma Co., Ltd. | $1.48B | Small cap | +15.52% |
| 4516.T | Nippon Shinyaku Co., Ltd. | $1.46B | Small cap | +4.08% |
| ANAB | AnaptysBio, Inc. | $1.46B | Small cap | +102.20% |
| KALV | KalVista Pharmaceuticals Inc | $1.44B | Small cap | +140.43% |
| ETON | Eton Pharmaceuticals, Inc. | $1.43B | Small cap | +171.48% |
| TYRA | Tyra Biosciences, Inc. | $1.40B | Small cap | +37.60% |
| NKTR | Nektar Therapeutics | $1.28B | Small cap | −40.15% |
| SLN | Silence Therapeutics plc | $1.23B | Small cap | +177.03% |
| PYC.AX | PYC Therapeutics Limited | $1.21B | Small cap | +43.85% |
| AVLN | Avalyn Pharma Inc. | $1.20B | Small cap | −7.97% |
| OMER | Omeros Corporation | $1.18B | Small cap | +111.28% |
| 006280.KS | GC Biopharma Corp. | $1.14B | Small cap | +0.62% |
| MLTX | MoonLake Immunotherapeutics | $1.01B | Small cap | +17.28% |
| JBIO | Jade Biosciences, Inc. | $922.16M | Small cap | +42.30% |
| SVRA | Savara Inc. | $864.79M | Small cap | +3.20% |
| PHAR | Pharming Group N.V. | $842.26M | Small cap | −10.73% |
| ANNX | Annexon, Inc. | $701.44M | Small cap | +4.52% |
| DSGN | Design Therapeutics, Inc. | $647.09M | Small cap | +48.35% |
| GYRE | Gyre Therapeutics, Inc. | $643.62M | Small cap | −24.31% |
| WVE | Wave Life Sciences, Inc. | $632.52M | Small cap | −57.87% |
| CRMD | CorMedix Inc. | $618.88M | Small cap | −28.14% |
| DBVT | DBV Technologies S.A. | $612.77M | Small cap | −37.59% |
| ZVRA | Zevra Therapeutics, Inc. | $582.55M | Small cap | −13.99% |
| IRWD | Ironwood Pharmaceuticals, Inc. | $578.34M | Small cap | +114.72% |
| 005257.KS | GC Corp. | $565.94M | Small cap | −33.38% |
| STTK | Shattuck Labs, Inc. | $550.99M | Small cap | +168.93% |
| VALN | Valneva SE | $512.99M | Small cap | −41.58% |
| CLYM | Climb Bio, Inc. | $506.01M | Small cap | +319.52% |
| AQST | Aquestive Therapeutics, Inc. | $502.05M | Small cap | −43.29% |
| KMDA | Kamada Ltd. | $458.22M | Small cap | +16.37% |
| AGMB | AgomAb Therapeutics NV | $422.06M | Small cap | −41.50% |
| ASMB | Assembly Biosciences, Inc. | $400.49M | Small cap | −33.99% |
| 4552.T | JCR Pharmaceuticals Co., Ltd. | $400.36M | Small cap | −13.24% |
| TECX | Tectonic Therapeutic, Inc. | $390.01M | Small cap | +7.14% |
| SPRY | ARS Pharmaceuticals, Inc. | $389.83M | Small cap | −59.00% |
| RZLT | Rezolute, Inc. | $369.48M | Small cap | −59.58% |
| AVTX | Avalo Therapeutics, Inc. | $363.08M | Small cap | −62.37% |
| ZURA | Zura Bio Limited | $341.15M | Small cap | −9.41% |
| ENTA | Enanta Pharmaceuticals, Inc. | $339.02M | Small cap | +14.29% |
| AVIR | Atea Pharmaceuticals, Inc. | $333.65M | Small cap | +28.00% |
| XFOR | X4 Pharmaceuticals, Inc. | $322.23M | Small cap | −13.10% |
| TTRX | Turn Therapeutics Inc. | $322.20M | Small cap | +113.48% |
| FULC | Fulcrum Therapeutics, Inc. | $278.03M | Small cap | −62.28% |
| QTTB | Q32 Bio Inc. | $251.55M | Small cap | +201.79% |
| CUV.AX | Clinuvel Pharmaceuticals Limited | $248.43M | Small cap | −38.51% |
| LRMR | Larimar Therapeutics, Inc. | $244.12M | Small cap | −48.39% |
| IFRX | InflaRx N.V. | $232.10M | Small cap | −5.12% |
| SLGL | Sol-Gel Technologies Ltd. | $227.38M | Small cap | +74.91% |
| KROS | Keros Therapeutics, Inc. | $224.64M | Small cap | −24.62% |
| SIGA | SIGA Technologies, Inc. | $224.17M | Small cap | −57.69% |
| IKT | Inhibikase Therapeutics, Inc. | $212.09M | Small cap | −2.56% |
| CAMP | CAMP4 THERAPEUTICS CORPORATION | $201.44M | Small cap | −17.69% |
| PLX | Protalix BioTherapeutics, Inc. | $199.82M | Small cap | +4.20% |
| 0AB6.L | Hyloris Pharmaceuticals SA | $185.32M | Small cap | −28.56% |
| TRDA | Entrada Therapeutics, Inc. | $184.95M | Small cap | −35.02% |
| PRQR | ProQR Therapeutics N.V. | $182.04M | Small cap | −56.64% |
| IVVD | Invivyd, Inc. | $180.81M | Small cap | −72.60% |
| ELDN | Eledon Pharmaceuticals, Inc. | $179.59M | Small cap | −42.30% |
| AKBA | Akebia Therapeutics, Inc. | $178.40M | Small cap | −79.69% |
| PEPG | PepGen Inc. | $172.46M | Small cap | −54.14% |
| SION | Sionna Therapeutics, Inc. | $166.83M | Small cap | −90.37% |
| MDWD | MediWound Ltd. | $155.76M | Small cap | −34.41% |
| UPB | Upstream Bio, Inc. | $150.62M | Small cap | −88.34% |
| RNA | Atrium Therapeutics, Inc. | $140.27M | Small cap | −45.42% |
| ANTX | AN2 Therapeutics, Inc. | $133.96M | Small cap | +168.89% |
| SPRB | Spruce Biosciences, Inc. | $129.76M | Small cap | −64.24% |
| ARMP | Armata Pharmaceuticals, Inc. | $128.28M | Small cap | −34.54% |
| PAR.AX | Paradigm Biopharmaceuticals Limited | $107.73M | Small cap | −44.94% |
| PYPD | PolyPid Ltd. | $106.64M | Small cap | +46.54% |
| UNCY | Unicycive Therapeutics, Inc. | $98.07M | Micro cap | −31.68% |
| INO | Inovio Pharmaceuticals, Inc. | $92.76M | Micro cap | −65.07% |
| RLYB | Rallybio Corporation | $88.40M | Micro cap | +233.00% |
| PLYX | Polaryx Therapeutics, Inc. | $86.16M | Micro cap | −94.80% |
| DXB.AX | Dimerix Limited | $84.29M | Micro cap | −60.78% |
| MIST | Milestone Pharmaceuticals Inc. | $80.23M | Micro cap | −66.26% |
| EQ | Equillium, Inc. | $79.26M | Micro cap | −8.76% |
| TELO | Telomir Pharmaceuticals, Inc. | $73.51M | Micro cap | −36.40% |
| FBIOP | Fortress Biotech, Inc. | $71.45M | Micro cap | +130.77% |
| RCE.AX | Recce Pharmaceuticals Ltd | $69.76M | Micro cap | −21.69% |
| RFL | Rafael Holdings, Inc. | $68.12M | Micro cap | −12.59% |
| CPIX | Cumberland Pharmaceuticals Inc. | $65.18M | Micro cap | +36.36% |
| ILA.AX | Island Pharmaceuticals Limited | $64.39M | Micro cap | −21.52% |
| TENX | Tenax Therapeutics, Inc. | $64.37M | Micro cap | −78.13% |
| FBIO | Fortress Biotech, Inc. | $62.37M | Micro cap | −27.24% |
| SPRO | Spero Therapeutics, Inc. | $62.31M | Micro cap | −53.28% |
| PTHS | Pelthos Therapeutics Inc. | $58.19M | Micro cap | −52.50% |
| 4599.T | StemRIM | $56.89M | Micro cap | −48.61% |
| GOSS | Gossamer Bio, Inc. | $55.96M | Micro cap | +282.85% |
| RNTX | Rein Therapeutics Inc. | $50.31M | Micro cap | −56.80% |
| 520A.T | J-Pharma Co., Ltd. | $49.31M | Micro cap | −41.86% |
| IMA | ImageneBio, Inc. | $45.97M | Micro cap | −51.50% |
| NSRX | Nasus Pharma Ltd. | $40.88M | Micro cap | −56.10% |
| GRCE | Grace Therapeutics, Inc. | $38.08M | Micro cap | −42.54% |
| SCYX | SCYNEXIS, Inc. | $37.91M | Micro cap | +405.98% |
| EDSA | Edesa Biotech, Inc. | $34.99M | Micro cap | −1.52% |
| NNVC | NanoViricides, Inc. | $34.73M | Micro cap | −15.53% |
| QNCX | Quince Therapeutics Inc | $32.27M | Micro cap | +84.80% |
| 4884.T | Kringle Pharma, Inc. | $30.61M | Micro cap | +36.08% |
| BRNS | Barinthus Biotherapeutics PLC | $30.23M | Micro cap | −41.73% |
| BOT.AX | Botanix Pharmaceuticals Limited | $25.20M | Micro cap | −90.71% |
| AARD | Aardvark Therapeutics, Inc. | $23.64M | Micro cap | −90.76% |
| 4591.T | Ribomic Inc. | $23.33M | Micro cap | −29.03% |
| MCRB | Seres Therapeutics, Inc. | $19.89M | Micro cap | −88.47% |
| QNRX | Quoin Pharmaceuticals, Ltd. | $19.26M | Micro cap | −69.62% |
| VYNE | VYNE Therapeutics Inc | $19.07M | Micro cap | +7811.36% |
| COCP | Cocrystal Pharma, Inc. | $18.72M | Micro cap | −20.98% |
| JSPR | Jasper Therapeutics, Inc. | $16.82M | Micro cap | −78.31% |
| ATYR | aTyr Pharma, Inc. | $15.05M | Micro cap | −84.23% |
| 4881.T | FunPep Company Limited | $13.83M | Micro cap | −56.57% |
| KTTA | Pasithea Therapeutics Corp. | $13.36M | Micro cap | −43.52% |
| HIND | Vyome Holdings, Inc. | $12.56M | Micro cap | −69.02% |
| TVRD | Tvardi Therapeutics, Inc. | $11.23M | Micro cap | −82.71% |
| AZTR | Azitra, Inc. | $9.27M | Micro cap | +180.22% |
| IMC.AX | Immuron Limited | $9.06M | Micro cap | −56.52% |
| CALC | CalciMedica, Inc. | $8.88M | Micro cap | −57.10% |
| INM | InMed Pharmaceuticals Inc. | $8.74M | Micro cap | −22.06% |
| SNGX | Soligenix, Inc. | $7.94M | Micro cap | −77.56% |
| IMRN | Immuron Limited | $7.43M | Micro cap | −58.18% |
| CMMB | Chemomab Therapeutics Ltd. | $7.33M | Micro cap | −67.21% |
| XCUR | Exicure, Inc. | $7.14M | Micro cap | −76.71% |
| PULM | Pulmatrix, Inc. | $5.26M | Micro cap | −70.79% |
| GLMD | Galmed Pharmaceuticals Ltd. | $4.95M | Micro cap | +162.32% |
| JAGX | Jaguar Health, Inc. | $3.97M | Micro cap | −96.70% |
| VBS.AX | Vectus Biosystems Limited | $3.93M | Micro cap | −35.71% |
| BIT.AX | Biotron Limited | $3.91M | Micro cap | −33.33% |
| GRI | GRI Bio, Inc. | $3.28M | Micro cap | −97.35% |
| SXTP | 60 Degrees Pharmaceuticals, Inc. | $3.05M | Micro cap | −85.34% |
| CVKD | Cadrenal Therapeutics, Inc. | $2.82M | Micro cap | −93.05% |
| ANR.AX | Anatara Lifesciences Ltd | $2.00M | Micro cap | −35.71% |
| XRTX | XORTX Therapeutics Inc. | $1.93M | Micro cap | −68.02% |
| VBIO | Valion Bio, Inc. | $1.76M | Micro cap | −70.00% |
| MTNB | Matinas BioPharma Holdings, Inc. | $1.63M | Micro cap | +8.36% |
| 0R55.L | BioSenic S.A. | $26.40K | Micro cap | −20.00% |
| 0A8U.L | Synlogic, Inc. | — | — | −38.22% |
| 0A9G.L | Mereo BioPharma Group plc | — | — | −86.42% |
| 1AE.DE | argenx SE | — | — | +0.19% |
| A1RG34.SA | argenx SE | — | Mega cap | −9.29% |
| A2RR34.SA | Arrowhead Pharmaceuticals, Inc. | — | Mid cap | +36.34% |
| ABNX.PA | ABIONYX Pharma SA | — | Small cap | −53.55% |
| ABVX.PA | ABIVAX Société Anonyme | — | Mid cap | −1.08% |
| ALBPS.PA | Biophytis S.A. | — | — | −71.04% |
| ALDVI.PA | Advicenne S.A. | — | — | −61.72% |
| ALNEV.PA | Neovacs S.A. | — | — | −31.82% |
| ALTHX.PA | THX Pharma Société Anonyme | — | — | +27.91% |
| ANNX.ST | Annexin Pharmaceuticals AB (publ) | — | Small cap | −68.45% |
| APLI.TO | Appili Therapeutics Inc. | — | — | −66.67% |
| APTA.ST | Aptahem AB (publ) | — | — | −79.45% |
| B1MR34.SA | BioMarin Pharmaceutical Inc. | — | Large cap | −0.89% |
| BIOSGN.ST | Biosergen AB (publ) | — | — | −99.01% |
| BIOV.SW | BioVersys AG | — | — | +2.90% |
| BPBS.PA | BIOPHYTIS BSA | — | — | 0.00% |
| BSLN.SW | Basilea Pharmaceutica AG | — | — | +39.09% |
| CAMX.ST | Camurus AB (publ) | — | Large cap | −2.63% |
| CESSA.CO | Cessatech A/S | — | — | −49.04% |
| CRDL.TO | Cardiol Therapeutics Inc. | — | Small cap | −5.88% |
| CRNO-B.ST | Cereno Scientific AB (publ) | — | Small cap | −57.04% |
| CURN.SW | Curatis Holding AG | — | — | +36.80% |
| DBV.PA | DBV Technologies S.A. | — | Small cap | −41.82% |
| EPRX.TO | Eupraxia Pharmaceuticals Inc. | — | Small cap | +26.16% |
| GNFT.PA | Genfit S.A. | — | Small cap | +128.93% |
| IMM.L | ImmuPharma plc | — | — | −65.96% |
| MDP.TO | Medexus Pharmaceuticals Inc. | — | Small cap | +68.51% |
| MSCL.TO | Satellos Bioscience Inc. | — | Small cap | +12.68% |
| PHGN.DE | Pharming Group N.V. | — | — | −31.40% |
| PHR.WA | Pharmena S.A. | — | — | −12.57% |
| REC.MI | Recordati Industria Chimica e Farmaceutica S.p.A. | — | Large cap | +5.26% |
| RVX.TO | Resverlogix Corp. | — | — | −20.00% |
| SANN.SW | Santhera Pharmaceuticals Holding AG | — | — | +37.07% |
| STX.L | Shield Therapeutics plc | — | Small cap | −30.07% |
| VRTX34.SA | Vertex Pharmaceuticals Incorporated | — | Mega cap | −84.64% |
Covers ~23,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Price and the 52-week distance are in the currency the stock trades in; only market values are converted.
We cover 227 companies grouped under the Rare disease theme. The median market value in the group is $340.09M. Among the 164 with a price from the latest session, the median move over the past trading day is +0.06%. 25% of the 214 with a 200-day average trade above it. Price change over the past year runs from −70.9% to +112.2% across the middle 80 percent of the group, with a median of −14.5%. Across the group, 1 company currently carries a tier A volume signal.