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Rare disease stocks

We cover 65 companies grouped under the Rare disease theme. The median market value in the group is $264.31M. Across the group, the median move over the past trading day is 0.00%. 53% of the 57 with a 200-day average trade above it. Price change over the past year runs from −53.5% to +87.6% across the middle 80 percent of the group, with a median of −3.1%. Across the group, 1 company currently carries a tier A volume signal.

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Table

65 of 268 companies match these filters.Clear filters

TickerCompanyMarket cap (USD)Size1Y return
VX1.DEVertex Pharmaceuticals Incorporated$140.77BLarge cap+40.14%
0QZU.LVertex Pharmaceuticals Incorporated$112.52BLarge cap+42.39%
0HD2.LAlnylam Pharmaceuticals, Inc.$35.05BLarge cap−46.85%
DUL.DEAlnylam Pharmaceuticals, Inc.$31.87BLarge cap−11.75%
0JAV.LInsmed Incorporated$12.89BLarge cap−6.25%
REC.MIRecordati Industria Chimica e Farmaceutica S.p.A.$12.60BLarge cap+2.09%
ABVX.PAABIVAX Société Anonyme$10.42BLarge cap+42.59%
0JDI.LIonis Pharmaceuticals, Inc.$10.40BLarge cap+49.07%
0HNC.LBioMarin Pharmaceutical Inc.$9.93BMid cap+12.68%
0HI3.LArrowhead Pharmaceuticals, Inc.$6.98BMid cap+317.86%
CAMX.STCamurus AB (publ)$3.87BMid cap−14.52%
0RD1.LCamurus AB (publ)$2.84BMid cap−13.50%
0L35.LSarepta Therapeutics, Inc.$1.69BSmall cap+4.63%
0LIF.LUltragenyx Pharmaceutical Inc.$1.40BSmall cap−11.63%
0HB0.LAgios Pharmaceuticals, Inc.$1.19BSmall cap−14.25%
DBV.PADBV Technologies S.A.$928.30MSmall cap+54.11%
GNFT.PAGenfit S.A.$836.50MSmall cap+293.99%
0QNA.LBasilea Pharmaceutica AG$762.45MSmall cap+38.97%
AYJ.DEValneva SE$659.69MSmall cap−25.10%
0KBU.LOmeros Corporation$575.28MSmall cap+341.05%
0OB3.LValneva SE$270.41MSmall cap−24.84%
XUP.DEGenfit S.A.$258.22MSmall cap+166.82%
0QN1.LSanthera Pharmaceuticals Holding AG$254.58MSmall cap+12.30%
0T6G.LQ32 Bio Inc.$246.69MSmall cap
0AB6.LHyloris Pharmaceuticals SA$185.32MSmall cap−32.01%
CRNO-B.STCereno Scientific AB (publ)$155.36MSmall cap−53.95%
0H8T.LAclaris Therapeutics, Inc.$122.82MSmall cap+265.21%
ABNX.PAABIONYX Pharma SA$97.56MMicro cap−16.20%
0RAG.LABIONYX Pharma SA$95.77MMicro cap−18.26%
STX.LShield Therapeutics plc$70.81MMicro cap−41.98%
ALTHX.PATHX Pharma Société Anonyme$70.40MMicro cap+89.35%
0IIM.LEsperion Therapeutics, Inc.$61.56MMicro cap+46.64%
ALDVI.PAAdvicenne S.A.$29.99MMicro cap+41.44%
IMM.LImmuPharma plc$29.03MMicro cap+83.56%
0RQJ.LSaniona AB (publ)$27.98MMicro cap−13.86%
ALBPS.PABiophytis S.A.$12.86MMicro cap−53.47%
ANNX.STAnnexin Pharmaceuticals AB (publ)$10.31MMicro cap−49.23%
PHR.WAPharmena S.A.$9.49MMicro cap−7.51%
BIOSGN.STBiosergen AB (publ)$5.62MMicro cap−95.33%
APTA.STAptahem AB (publ)$1.53MMicro cap−72.50%
0R55.LBioSenic S.A.$26.40KMicro cap−23.08%
ALNEV.PANeovacs S.A.$29.00Micro cap−11.54%
0A43.LInovio Pharmaceuticals, Inc.−45.78%
0A4D.LEquillium, Inc.+24.24%
0A6I.LSoligenix, Inc.−86.94%
0A8E.LXeris Biopharma Holdings, Inc.+10.09%
0A8U.LSynlogic, Inc.−15.17%
0A9G.LMereo BioPharma Group plc−83.87%
0ABW.LEgetis Therapeutics AB (publ)+49.12%
0D1W.LBiophytis S.A.−53.43%
0JQ2.LKALA BIO, Inc.−99.82%
0K1R.LViridian Therapeutics, Inc.+31.82%
0L49.LSCYNEXIS, Inc.+543.07%
0QNS.LCURATIS AG CURATIS AG AG ORD SH−15.04%
0UNL.LNEKTAR THERAPEUTICS NEKTAR THER+14.54%
1AE.DEargenx SE+35.39%
2X1.DEABIVAX Société Anonyme+35.69%
BIOV.SWBioVersys AG−8.49%
BPBS.PABIOPHYTIS BSA0.00%
BSLN.SWBasilea Pharmaceutica AG+38.40%
CESSA.COCessatech A/S−46.63%
CURN.SWCuratis Holding AG+73.80%
DBV.DEDBV Technologies S.A.+61.15%
PHGN.DEPharming Group N.V.−21.41%
SANN.SWSanthera Pharmaceuticals Holding AG+15.63%

Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.

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