Free tool
Rare disease stocks
We cover 90 companies grouped under the Rare disease theme. The median market value in the group is $42.85M. Across the group, the median move over the past trading day is −0.06%. 39% of the 87 with a 200-day average trade above it. Price change over the past year runs from −88.9% to +109.3% across the middle 80 percent of the group, with a median of −26.4%.
Other lists in this group
SaaSAI applicationsCybersecuritySemiconductor designSemiconductor equipmentFintech softwarePayment processingEcommerce marketplacesStreaming mediaGaming softwareOncologyRare diseaseMedical devicesCell therapyDiagnosticsRegional banksAsset managementGold miningCryptocurrency and digital assetsSpecialty chemicalsAll stocks
Table
90 of 268 companies match these filters.Clear filters
| Ticker | Company | Price | 1M return | YTD return | 1Y return |
|---|---|---|---|---|---|
| VX1.DE | Vertex Pharmaceuticals Incorporated | 475.00 EUR | +10.21% | +23.55% | +41.64% |
| VRTX34.SA | Vertex Pharmaceuticals Incorporated | 88.56 BRL | +14.82% | −85.60% | −83.18% |
| VRTX | Vertex Pharmaceuticals Incorporated | $547.29 | +11.60% | +21.05% | +40.66% |
| ARGX | argenx SE | $1,047.10 | +20.05% | +24.66% | +47.90% |
| A1RG34.SA | argenx SE | 209.16 BRL | +14.71% | +11.37% | +36.97% |
| DUL.DE | Alnylam Pharmaceuticals, Inc. | 204.00 EUR | −19.59% | −40.19% | −10.21% |
| ALNY | Alnylam Pharmaceuticals, Inc. | $239.00 | −17.13% | −40.28% | −47.38% |
| A1LN34.SA | Alnylam Pharmaceuticals, Inc. | 62.25 BRL | −15.31% | −44.14% | −49.35% |
| INSM | Insmed Incorporated | $124.39 | +19.46% | −29.77% | −7.54% |
| ROIV | Roivant Sciences Ltd. | $36.75 | +8.60% | +67.58% | +206.51% |
| JAZZ | Jazz Pharmaceuticals plc | $249.29 | −2.97% | +43.97% | +100.35% |
| ASND | Ascendis Pharma A/S | $250.25 | −1.65% | +17.33% | +29.66% |
| BBIO | BridgeBio Pharma, Inc. | $79.37 | −7.22% | +1.45% | +60.05% |
| CORT | Corcept Therapeutics Incorporated | $119.80 | +27.19% | +213.61% | +71.81% |
| BMRN | BioMarin Pharmaceutical Inc. | $65.61 | +5.70% | +10.36% | +11.85% |
| REC.MI | Recordati Industria Chimica e Farmaceutica S.p.A. | 52.70 EUR | +2.53% | +10.68% | +1.80% |
| B1MR34.SA | BioMarin Pharmaceutical Inc. | 166.77 BRL | +12.08% | −0.14% | +4.97% |
| ARWR | Arrowhead Pharmaceuticals, Inc. | $89.12 | +3.89% | +31.46% | +308.99% |
| CYTK | Cytokinetics, Incorporated | $79.20 | −0.31% | +28.30% | +109.36% |
| IONS | Ionis Pharmaceuticals, Inc. | $63.36 | +14.58% | −20.47% | +48.21% |
| KYMR | Kymera Therapeutics, Inc. | $125.55 | +18.26% | +72.55% | +197.09% |
| ABVX.PA | ABIVAX Société Anonyme | 102.30 EUR | −5.63% | −11.04% | +48.91% |
| ABNX.PA | ABIONYX Pharma SA | 1.97 EUR | +5.79% | −49.58% | −31.34% |
| ILA.AX | Island Pharmaceuticals Limited | 0.45 AUD | +18.42% | +3.45% | +109.30% |
| FBIO | Fortress Biotech, Inc. | $2.81 | −17.11% | −30.27% | +20.09% |
| PLYX | Polaryx Therapeutics, Inc. | $2.09 | +5.03% | −94.03% | −94.03% |
| PAR.AX | Paradigm Biopharmaceuticals Limited | 0.22 AUD | +30.30% | −36.76% | −24.56% |
| RLYB | Rallybio Corporation | $16.88 | +4.49% | +198.44% | +257.63% |
| GOSS | Gossamer Bio, Inc. | $0.17 | −15.17% | −93.96% | −92.93% |
| RCE.AX | Recce Pharmaceuticals Ltd | 0.38 AUD | +2.74% | −43.82% | −10.71% |
| TELO | Telomir Pharmaceuticals, Inc. | $1.17 | −0.85% | −12.69% | −20.95% |
| TENX | Tenax Therapeutics, Inc. | $2.12 | −86.58% | −80.81% | −64.19% |
| STX.L | Shield Therapeutics plc | 4.85 GBP | −15.65% | −50.76% | −37.42% |
| FBIOP | Fortress Biotech, Inc. | $18.40 | −1.92% | +81.10% | +131.74% |
| ALTHX.PA | THX Pharma Société Anonyme | 4.18 EUR | +5.16% | +83.92% | +73.96% |
| SPRO | Spero Therapeutics, Inc. | $1.22 | +2.09% | −48.09% | −38.38% |
| RNTX | Rein Therapeutics Inc. | $0.80 | +2.30% | −36.00% | −27.27% |
| IMA | ImageneBio, Inc. | $5.43 | −5.73% | −19.67% | −60.19% |
| SCYX | SCYNEXIS, Inc. | $5.67 | +56.20% | +787.32% | +579.04% |
| ATYR | aTyr Pharma, Inc. | $0.55 | +11.54% | −27.40% | −89.34% |
| NSRX | Nasus Pharma Ltd. | $4.05 | +33.66% | −46.36% | −49.75% |
| MCRB | Seres Therapeutics, Inc. | $4.76 | −0.83% | −68.58% | −74.79% |
| EDSA | Edesa Biotech, Inc. | $4.94 | −0.60% | +229.33% | +105.83% |
| GRCE | Grace Therapeutics, Inc. | $2.15 | −4.44% | −41.26% | −29.97% |
| MREO | Mereo BioPharma Group plc | $0.28 | −10.03% | −45.49% | −84.20% |
| BOT.AX | Botanix Pharmaceuticals Limited | 0.02 AUD | +5.26% | −85.19% | −86.67% |
| NNVC | NanoViricides, Inc. | $1.28 | −20.50% | +5.79% | −9.86% |
| QNCX | Quince Therapeutics, Inc. | $31.31 | +61.64% | +4.37% | +100.71% |
| IMM.L | ImmuPharma plc | 3.41 GBP | −24.22% | −45.00% | +89.66% |
| 520A.T | J-PHARMACEUTICALS CO LTD | 280.00 JPY | +4.09% | −60.00% | −60.00% |
| ALDVI.PA | Advicenne S.A. | 1.75 EUR | +4.79% | −6.02% | +39.11% |
| 4591.T | Ribomic Inc. | 86.00 JPY | +21.13% | +10.26% | −17.31% |
| BRNS | Barinthus Biotherapeutics plc | $0.71 | +23.93% | −3.89% | −38.04% |
| RVX.TO | Resverlogix Corp. | 0.10 CAD | 0.00% | 0.00% | 0.00% |
| JSPR | Jasper Therapeutics, Inc. | $0.72 | +13.43% | −60.98% | −75.24% |
| TVRD | Tvardi Therapeutics, Inc. | $1.78 | −27.05% | −56.37% | −94.18% |
| 4884.T | Kringle Pharma, Inc. | 440.00 JPY | +42.86% | +12.24% | −11.29% |
| COCP | Cocrystal Pharma, Inc. | $1.12 | +20.43% | +13.13% | −27.74% |
| VYNE | VYNE Therapeutics Inc | $28.56 | +3080.40% | +4824.14% | +8660.74% |
| KTTA | Pasithea Therapeutics Corp. | $0.57 | +26.67% | −52.10% | −24.30% |
| CALC | CalciMedica, Inc. | $0.59 | −18.18% | −91.28% | −79.74% |
| CMMB | Chemomab Therapeutics Ltd. | $2.59 | +81.12% | +44.69% | −25.57% |
| 4881.T | FunPep Company Limited | 51.00 JPY | +2.00% | −37.04% | −55.65% |
| HIND | Vyome Holdings, Inc. | $2.16 | +8.54% | −39.15% | −79.68% |
| ALBPS.PA | Biophytis S.A. | 0.08 EUR | +422.88% | +28.41% | −50.31% |
| AZTR | Azitra, Inc. | $0.17 | +33.00% | −38.03% | −83.21% |
| QNRX | Quoin Pharmaceuticals, Ltd. | $5.18 | +23.33% | −63.21% | −29.81% |
| ANNX.ST | Annexin Pharmaceuticals AB (publ) | 13.60 SEK | +7.09% | −31.66% | −46.03% |
| PHR.WA | Pharmena S.A. | 3.14 PLN | +1.62% | +18.49% | −8.72% |
| IMRN | Immuron Limited | $1.14 | +4.11% | +43.40% | −35.77% |
| IMC.AX | Immuron Limited | 0.04 AUD | +8.82% | +5.71% | −46.38% |
| SNGX | Soligenix, Inc. | $0.38 | +6.67% | −72.96% | −87.20% |
| XCUR | Exicure, Inc. | $1.26 | −27.59% | −77.42% | −77.93% |
| INM | InMed Pharmaceuticals Inc. | $1.43 | −14.37% | +27.68% | −36.44% |
| VBS.AX | Vectus Biosystems Limited | 0.17 AUD | +30.77% | +3.03% | +104.82% |
| PULM | Pulmatrix, Inc. | $1.53 | −9.23% | −32.52% | −68.62% |
| BIOSGN.ST | Biosergen AB (publ) | 2.48 SEK | +262.31% | −93.80% | −94.62% |
| CVKD | Cadrenal Therapeutics, Inc. | $1.55 | −22.89% | −78.85% | −88.87% |
| JAGX | Jaguar Health, Inc. | $0.92 | −4.63% | −97.37% | −98.52% |
| GLMD | Galmed Pharmaceuticals Ltd. | $4.33 | +710.86% | +426.12% | +211.51% |
| GRI | GRI Bio, Inc. | $1.91 | +33.57% | −75.64% | −95.23% |
| XRTX | XORTX Therapeutics Inc. | $2.22 | +8.20% | −22.18% | −43.99% |
| BIT.AX | Biotron Limited | 0.00 AUD | −20.00% | −42.86% | −50.00% |
| SXTP | 60 Degrees Pharmaceuticals, Inc. | $1.08 | −28.00% | −47.67% | −78.23% |
| MTNB | Matinas BioPharma Holdings, Inc. | $0.20 | −32.97% | −68.32% | −90.08% |
| ANR.AX | Anatara Lifesciences Ltd | 0.01 AUD | −10.00% | −35.71% | 0.00% |
| APTA.ST | Aptahem AB (publ) | 0.56 SEK | −15.96% | −51.69% | −67.65% |
| APLI.TO | Appili Therapeutics Inc. | 0.02 CAD | +50.00% | −40.00% | −25.00% |
| VBIO | Valion Bio, Inc. | $0.16 | −45.83% | −89.01% | −94.92% |
| ALNEV.PA | Neovacs S.A. | 0.55 EUR | −31.22% | +6150.00% | −11.29% |
Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.