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Rare disease stocks
We cover 92 companies grouped under the Rare disease theme. The median market value in the group is $2.18B. Across the group, the median move over the past trading day is +1.38%. 56% of the 89 with a 200-day average trade above it. Price change over the past year runs from −86.7% to +208.8% across the middle 80 percent of the group, with a median of +34.7%.
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Table
92 of 268 companies match these filters.Clear filters
| Ticker | Company | Market cap (USD) | Size | 1Y return |
|---|---|---|---|---|
| VRTX | Vertex Pharmaceuticals Incorporated | $140.04B | Large cap | +42.14% |
| ARGX | argenx SE | $63.78B | Large cap | +50.52% |
| ALNY | Alnylam Pharmaceuticals, Inc. | $32.12B | Large cap | −45.88% |
| INSM | Insmed Incorporated | $27.07B | Large cap | −3.45% |
| ROIV | Roivant Sciences Ltd. | $26.26B | Large cap | +213.32% |
| JAZZ | Jazz Pharmaceuticals plc | $16.89B | Large cap | +108.87% |
| ASND | Ascendis Pharma A/S | $16.59B | Large cap | +32.89% |
| BBIO | BridgeBio Pharma, Inc. | $15.85B | Large cap | +70.01% |
| CORT | Corcept Therapeutics Incorporated | $13.36B | Large cap | +79.56% |
| BMRN | BioMarin Pharmaceutical Inc. | $12.80B | Large cap | +13.03% |
| ARWR | Arrowhead Pharmaceuticals, Inc. | $12.52B | Large cap | +329.16% |
| CYTK | Cytokinetics, Incorporated | $10.77B | Large cap | +109.29% |
| IONS | Ionis Pharmaceuticals, Inc. | $10.56B | Large cap | +52.01% |
| KYMR | Kymera Therapeutics, Inc. | $10.53B | Large cap | +202.82% |
| PTGX | Protagonist Therapeutics, Inc. | $10.01B | Large cap | +164.75% |
| CRNX | Crinetics Pharmaceuticals, Inc. | $9.00B | Mid cap | +182.02% |
| IMVT | Immunovant, Inc. | $8.95B | Mid cap | +192.14% |
| RYTM | Rhythm Pharmaceuticals, Inc. | $7.78B | Mid cap | +14.26% |
| SRRK | Scholar Rock Holding Corporation | $7.09B | Mid cap | +74.77% |
| ORKA | Oruka Therapeutics, Inc. | $6.74B | Mid cap | +601.72% |
| LQDA | Liquidia Corporation | $6.31B | Mid cap | +168.53% |
| KNSA | Kiniksa Pharmaceuticals International, plc | $6.17B | Mid cap | +142.74% |
| PTCT | PTC Therapeutics, Inc. Common Stock | $6.13B | Mid cap | +49.03% |
| DNTH | Dianthus Therapeutics, Inc. | $6.13B | Mid cap | +378.90% |
| TVTX | Travere Therapeutics, Inc. | $6.06B | Mid cap | +288.91% |
| MIRM | Mirum Pharmaceuticals, Inc. | $5.98B | Mid cap | +36.58% |
| GRFS | Grifols, S.A. | $5.44B | Mid cap | −17.62% |
| DYN | Dyne Therapeutics, Inc. | $4.92B | Mid cap | +102.62% |
| EWTX | Edgewise Therapeutics, Inc. | $4.80B | Mid cap | +209.16% |
| AMLX | Amylyx Pharmaceuticals, Inc. | $4.17B | Mid cap | +340.71% |
| MANE | Veradermics, Incorporated | $4.11B | Mid cap | +171.13% |
| CPRX | Catalyst Pharmaceuticals Inc | $3.85B | Mid cap | +52.72% |
| CLDX | Celldex Therapeutics, Inc. | $3.24B | Mid cap | +87.96% |
| IRON | Disc Medicine, Inc. | $3.16B | Mid cap | +38.71% |
| ARQT | Arcutis Biotherapeutics, Inc. | $3.12B | Mid cap | +58.44% |
| VRDN | Viridian Therapeutics, Inc. | $2.74B | Mid cap | +30.21% |
| PHVS | Pharvaris N.V. | $2.62B | Mid cap | +57.76% |
| RARE | Ultragenyx Pharmaceutical Inc. | $2.61B | Mid cap | −9.60% |
| TRVI | Trevi Therapeutics, Inc. | $2.56B | Mid cap | +146.57% |
| VERA | Vera Therapeutics, Inc. | $2.54B | Mid cap | +65.32% |
| NKTR | Nektar Therapeutics | $2.52B | Mid cap | +176.20% |
| BCRX | BioCryst Pharmaceuticals, Inc. | $2.51B | Mid cap | +17.16% |
| MLYS | Mineralys Therapeutics, Inc. | $2.32B | Mid cap | +78.70% |
| COAG | Hemab Therapeutics Holdings, Inc. | $2.32B | Mid cap | +46.03% |
| AUPH | Aurinia Pharmaceuticals Inc. | $2.23B | Mid cap | +38.03% |
| ZBIO | Zenas BioPharma, Inc. | $2.20B | Mid cap | +103.93% |
| STOK | Stoke Therapeutics, Inc. | $2.16B | Mid cap | +77.32% |
| ADMA | ADMA Biologics, Inc. | $2.14B | Mid cap | −42.86% |
| PVLA | Palvella Therapeutics, Inc. | $2.14B | Mid cap | +195.71% |
| GOSS | Gossamer Bio, Inc. | $99.97M | Micro cap | −91.33% |
| FBIO | Fortress Biotech, Inc. | $94.38M | Micro cap | +23.58% |
| PLYX | Polaryx Therapeutics, Inc. | $94.21M | Micro cap | −94.66% |
| RLYB | Rallybio Corporation | $89.67M | Micro cap | +262.65% |
| TENX | Tenax Therapeutics, Inc. | $86.82M | Micro cap | −60.81% |
| TELO | Telomir Pharmaceuticals, Inc. | $81.15M | Micro cap | −19.18% |
| FBIOP | Fortress Biotech, Inc. | $71.45M | Micro cap | +141.55% |
| SPRO | Spero Therapeutics, Inc. | $70.76M | Micro cap | −33.51% |
| RNTX | Rein Therapeutics Inc. | $69.01M | Micro cap | −32.20% |
| IMA | ImageneBio, Inc. | $63.80M | Micro cap | −60.78% |
| ATYR | aTyr Pharma, Inc. | $55.91M | Micro cap | −88.95% |
| SCYX | SCYNEXIS, Inc. | $51.64M | Micro cap | +514.20% |
| NSRX | Nasus Pharma Ltd. | $48.01M | Micro cap | −48.69% |
| MCRB | Seres Therapeutics, Inc. | $46.81M | Micro cap | −74.00% |
| GRCE | Grace Therapeutics, Inc. | $46.28M | Micro cap | −32.31% |
| MREO | Mereo BioPharma Group plc | $44.97M | Micro cap | −83.82% |
| EDSA | Edesa Biotech, Inc. | $42.90M | Micro cap | +83.88% |
| QNCX | Quince Therapeutics, Inc. | $34.05M | Micro cap | +95.76% |
| NNVC | NanoViricides, Inc. | $32.93M | Micro cap | −12.84% |
| BRNS | Barinthus Biotherapeutics plc | $26.96M | Micro cap | −44.77% |
| JSPR | Jasper Therapeutics, Inc. | $23.96M | Micro cap | −75.67% |
| TVRD | Tvardi Therapeutics, Inc. | $23.74M | Micro cap | −93.77% |
| COCP | Cocrystal Pharma, Inc. | $21.77M | Micro cap | −26.62% |
| VYNE | VYNE Therapeutics Inc | $19.07M | Micro cap | +8687.69% |
| KTTA | Pasithea Therapeutics Corp. | $18.71M | Micro cap | −21.90% |
| CALC | CalciMedica, Inc. | $17.10M | Micro cap | −78.92% |
| CMMB | Chemomab Therapeutics Ltd. | $16.85M | Micro cap | −33.91% |
| HIND | Vyome Holdings, Inc. | $15.65M | Micro cap | −80.23% |
| QNRX | Quoin Pharmaceuticals, Ltd. | $10.18M | Micro cap | −31.02% |
| AZTR | Azitra, Inc. | $9.55M | Micro cap | −78.97% |
| IMRN | Immuron Limited | $9.20M | Micro cap | −36.84% |
| SNGX | Soligenix, Inc. | $8.81M | Micro cap | −87.06% |
| XCUR | Exicure, Inc. | $7.79M | Micro cap | −79.90% |
| INM | InMed Pharmaceuticals Inc. | $7.69M | Micro cap | −35.43% |
| PULM | Pulmatrix, Inc. | $5.84M | Micro cap | −67.81% |
| JAGX | Jaguar Health, Inc. | $4.78M | Micro cap | −98.52% |
| CVKD | Cadrenal Therapeutics, Inc. | $4.74M | Micro cap | −87.58% |
| GLMD | Galmed Pharmaceuticals Ltd. | $4.48M | Micro cap | +205.34% |
| GRI | GRI Bio, Inc. | $4.28M | Micro cap | −95.14% |
| XRTX | XORTX Therapeutics Inc. | $4.11M | Micro cap | −44.74% |
| SXTP | 60 Degrees Pharmaceuticals, Inc. | $3.97M | Micro cap | −78.10% |
| MTNB | Matinas BioPharma Holdings, Inc. | $2.90M | Micro cap | −90.82% |
| VBIO | Valion Bio, Inc. | $660.05K | Micro cap | −95.00% |
Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.