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Rare disease stocks

We cover 42 companies grouped under the Rare disease theme. The median market value in the group is $264.31M. Across the group, the median move over the past trading day is +0.43%. 49% of the 39 with a 200-day average trade above it. Price change over the past year runs from −46.6% to +166.8% across the middle 80 percent of the group, with a median of −8.7%.

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Table

42 of 268 companies match these filters.Clear filters

TickerCompanyPrice1M returnYTD return1Y return
VX1.DEVertex Pharmaceuticals Incorporated475.00 EUR+10.21%+23.55%+41.64%
0QZU.LVertex Pharmaceuticals Incorporated$549.02+0.13%+22.11%+40.77%
0HD2.LAlnylam Pharmaceuticals, Inc.$241.82+0.67%−39.23%−46.60%
DUL.DEAlnylam Pharmaceuticals, Inc.204.00 EUR−19.59%−40.19%−10.21%
0JAV.LInsmed Incorporated$125.00+0.43%−28.28%−7.52%
REC.MIRecordati Industria Chimica e Farmaceutica S.p.A.52.70 EUR+2.53%+10.68%+1.80%
0JDI.LIonis Pharmaceuticals, Inc.$63.37+3.44%−19.72%+47.26%
ABVX.PAABIVAX Société Anonyme102.30 EUR−5.63%−11.04%+48.91%
0HNC.LBioMarin Pharmaceutical Inc.$66.19+0.05%+11.54%+15.03%
0HI3.LArrowhead Pharmaceuticals, Inc.$89.35+3.26%+32.80%+294.59%
CAMX.STCamurus AB (publ)615.00 SEK−1.68%+0.49%−15.35%
0RD1.LCamurus AB (publ)609.98 SEK−0.21%−0.53%−15.10%
0L35.LSarepta Therapeutics, Inc.$18.51+1.60%−13.25%−0.06%
0LIF.LUltragenyx Pharmaceutical Inc.$26.19+1.39%+12.52%−13.39%
0HB0.LAgios Pharmaceuticals, Inc.$34.05+0.18%+26.06%−13.00%
DBV.PADBV Technologies S.A.2.53 EUR+5.42%−22.51%+60.13%
GNFT.PAGenfit S.A.14.30 EUR+5.30%+172.38%+310.45%
0QNA.LBasilea Pharmaceutica AG65.80 CHF+2.73%+20.16%+41.96%
AYJ.DEValneva SE2.98 EUR+35.29%−23.93%−21.89%
0KBU.LOmeros Corporation$18.44−4.75%+11.14%+332.86%
0OB3.LValneva SE2.87 EUR+0.75%−23.95%−25.05%
XUP.DEGenfit S.A.14.08 EUR−1.81%+164.41%+166.82%
0QN1.LSanthera Pharmaceuticals Holding AG15.66 CHF−1.88%+29.00%+11.86%
0T6G.LQ32 Bio Inc.$16.34+7.94%
0AB6.LHyloris Pharmaceuticals SA4.38 EUR−1.79%−38.83%−33.23%
CRNO-B.STCereno Scientific AB (publ)4.71 SEK+0.13%−32.04%−53.59%
0H8T.LAclaris Therapeutics, Inc.$6.14−6.69%+105.92%+237.38%
ABNX.PAABIONYX Pharma SA1.97 EUR+5.79%−49.58%−31.34%
0RAG.LABIONYX Pharma SA2.01 EUR+3.40%−48.40%−29.10%
STX.LShield Therapeutics plc4.85 GBP−15.65%−50.76%−37.42%
ALTHX.PATHX Pharma Société Anonyme4.18 EUR+5.16%+83.92%+73.96%
0IIM.LEsperion Therapeutics, Inc.$3.19+0.14%−14.28%+44.65%
IMM.LImmuPharma plc3.41 GBP−24.22%−45.00%+89.66%
ALDVI.PAAdvicenne S.A.1.75 EUR+4.79%−6.02%+39.11%
0RQJ.LSaniona AB (publ)11.80 SEK+0.47%−44.08%−12.20%
ALBPS.PABiophytis S.A.0.08 EUR+422.88%+28.41%−50.31%
ANNX.STAnnexin Pharmaceuticals AB (publ)13.60 SEK+7.09%−31.66%−46.03%
PHR.WAPharmena S.A.3.14 PLN+1.62%+18.49%−8.72%
BIOSGN.STBiosergen AB (publ)2.48 SEK+262.31%−93.80%−94.62%
APTA.STAptahem AB (publ)0.56 SEK−15.96%−51.69%−67.65%
0R55.LBioSenic S.A.0.00 EUR0.00%−4.76%−25.93%
ALNEV.PANeovacs S.A.0.55 EUR−31.22%+6150.00%−11.29%

Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.

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