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Rare disease stocks
We cover 84 companies grouped under the Rare disease theme. The median market value in the group is $636.42M. Across the group, the median move over the past trading day is +1.74%. 65% of the 80 with a 200-day average trade above it. Price change over the past year runs from −36.5% to +234.2% across the middle 80 percent of the group, with a median of +42.1%.
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Table
84 of 268 companies match these filters.Clear filters
| Ticker | Company | Price | 1M return | YTD return | 1Y return | Next report |
|---|---|---|---|---|---|---|
| VX1.DE | Vertex Pharmaceuticals Incorporated | 469.95 EUR | +10.56% | +22.24% | +40.14% | Nov 2, 2026 |
| VRTX | Vertex Pharmaceuticals Incorporated | $552.85 | +15.42% | +22.28% | +42.14% | Nov 2, 2026 |
| 0QZU.L | Vertex Pharmaceuticals Incorporated | $554.44 | +1.12% | +23.31% | +42.39% | Nov 2, 2026 |
| ARGX | argenx SE | $1,019.49 | +14.70% | +21.37% | +50.52% | Oct 22, 2026 |
| 0HD2.L | Alnylam Pharmaceuticals, Inc. | $240.20 | −4.67% | −39.64% | −46.85% | Oct 29, 2026 |
| ALNY | Alnylam Pharmaceuticals, Inc. | $240.08 | −13.76% | −40.01% | −45.88% | Oct 29, 2026 |
| DUL.DE | Alnylam Pharmaceuticals, Inc. | 200.50 EUR | −20.91% | −41.22% | −11.75% | Oct 29, 2026 |
| INSM | Insmed Incorporated | $123.89 | +18.29% | −30.05% | −3.45% | Oct 29, 2026 |
| BBIO | BridgeBio Pharma, Inc. | $80.40 | −4.42% | +2.77% | +70.01% | Oct 28, 2026 |
| 0JAV.L | Insmed Incorporated | $125.32 | +0.69% | −28.09% | −6.25% | Oct 29, 2026 |
| BMRN | BioMarin Pharmaceutical Inc. | $66.12 | +9.71% | +11.22% | +13.03% | Oct 26, 2026 |
| CYTK | Cytokinetics, Incorporated | $77.46 | −3.92% | +25.48% | +109.29% | Nov 5, 2026 |
| KYMR | Kymera Therapeutics, Inc. | $126.64 | +15.07% | +74.05% | +202.82% | Nov 3, 2026 |
| ABVX.PA | ABIVAX Société Anonyme | 98.10 EUR | −9.83% | −14.70% | +42.59% | Sep 21, 2026 |
| PTGX | Protagonist Therapeutics, Inc. | $150.59 | +11.09% | +72.73% | +164.75% | Nov 5, 2026 |
| AGIO | Agios Pharmaceuticals, Inc. Common Stock | $33.90 | −8.30% | +24.72% | −9.02% | Oct 29, 2026 |
| SEPN | Septerna, Inc. | $41.30 | +23.32% | +47.61% | +245.32% | Nov 9, 2026 |
| ETON | Eton Pharmaceuticals, Inc. | $63.05 | +49.02% | +287.76% | +268.93% | Nov 12, 2026 |
| ANIP | ANI Pharmaceuticals, Inc. | $75.65 | −3.47% | −3.54% | −16.24% | Nov 6, 2026 |
| AVLN | Avalyn Pharma Inc. | $38.20 | +38.31% | +29.54% | +29.54% | Nov 16, 2026 |
| 0L35.L | Sarepta Therapeutics, Inc. | $18.94 | +3.95% | −11.24% | +4.63% | Nov 4, 2026 |
| MAZE | Maze Therapeutics, Inc. | $30.42 | +6.03% | −23.51% | +128.55% | Nov 5, 2026 |
| FBRX | Forte Biosciences, Inc. | $76.97 | +0.61% | +226.01% | +580.25% | Nov 9, 2026 |
| TRAX | First Tracks Biotherapeutics, Inc. | $45.11 | +7.33% | +137.42% | +137.42% | Nov 5, 2026 |
| XERS | Xeris Biopharma Holdings, Inc. | $8.74 | +6.46% | +18.91% | +12.48% | Nov 5, 2026 |
| TYRA | Tyra Biosciences, Inc. | $26.69 | −14.07% | −0.37% | +122.42% | Nov 4, 2026 |
| 0LIF.L | Ultragenyx Pharmaceutical Inc. | $26.69 | +3.33% | +14.67% | −11.63% | Nov 3, 2026 |
| OMER | Omeros Corporation | $19.28 | +70.02% | +17.70% | +343.22% | Nov 12, 2026 |
| JBIO | Jade Biosciences, Inc. | $21.84 | +9.47% | +54.24% | +176.46% | Nov 12, 2026 |
| MLTX | MoonLake Immunotherapeutics | $15.56 | −21.73% | +30.21% | −71.52% | Nov 5, 2026 |
| 0HB0.L | Agios Pharmaceuticals, Inc. | $33.99 | +2.11% | +25.84% | −14.25% | Oct 29, 2026 |
| SVRA | Savara Inc. | $5.60 | +3.13% | −0.71% | +78.34% | Nov 11, 2026 |
| ANNX | Annexon, Inc. | $5.15 | +0.39% | +9.81% | +139.53% | Nov 9, 2026 |
| DBVT | DBV Technologies S.A. | $14.97 | +7.70% | −21.42% | +52.91% | Oct 28, 2026 |
| DBV.PA | DBV Technologies S.A. | 2.44 EUR | +2.78% | −25.33% | +54.11% | Oct 28, 2026 |
| SLN | Silence Therapeutics plc | $13.67 | +13.26% | +122.28% | +170.16% | Nov 5, 2026 |
| GNFT.PA | Genfit S.A. | 13.90 EUR | +5.30% | +164.76% | +293.99% | Sep 29, 2026 |
| STTK | Shattuck Labs, Inc. | $8.06 | +14.49% | +117.25% | +710.87% | Nov 12, 2026 |
| TECX | Tectonic Therapeutic, Inc. | $37.71 | +23.20% | +80.34% | +53.48% | Nov 5, 2026 |
| ZVRA | Zevra Therapeutics, Inc. | $12.04 | +24.00% | +44.36% | +28.63% | Nov 4, 2026 |
| GYRE | Gyre Therapeutics, Inc. | $6.68 | +8.97% | −1.91% | −18.54% | Nov 5, 2026 |
| CRMD | CorMedix Inc. | $8.56 | +12.63% | −29.61% | −37.65% | Nov 16, 2026 |
| ZURA | Zura Bio Limited | $6.32 | +17.47% | +13.87% | +208.29% | Nov 12, 2026 |
| AQST | Aquestive Therapeutics, Inc. | $5.08 | +36.19% | −21.24% | +31.61% | Nov 4, 2026 |
| 0KBU.L | Omeros Corporation | $19.34 | −0.10% | +16.56% | +341.05% | Nov 12, 2026 |
| SPRY | ARS Pharmaceuticals, Inc. | $5.72 | −0.69% | −50.22% | −57.66% | Nov 10, 2026 |
| KMDA | Kamada Ltd. Ordinary Shares | $8.63 | +23.46% | +26.48% | +26.12% | Nov 9, 2026 |
| EPRX | Eupraxia Pharmaceuticals Inc. | $7.42 | +20.26% | −1.98% | +41.87% | Nov 3, 2026 |
| EPRX.TO | Eupraxia Pharmaceuticals Inc. | 10.20 CAD | +16.70% | −2.49% | +41.67% | Nov 3, 2026 |
| RZLT | Rezolute, Inc. | $5.01 | +1.42% | +131.41% | −28.43% | Sep 16, 2026 |
| AVIR | Atea Pharmaceuticals, Inc. | $5.43 | +12.66% | +56.03% | +48.36% | Nov 11, 2026 |
| LRMR | Larimar Therapeutics, Inc. | $4.16 | +8.62% | +19.88% | +11.83% | Nov 5, 2026 |
| XFOR | X4 Pharmaceuticals, Inc. | $4.16 | +5.58% | +6.94% | +4.79% | Nov 5, 2026 |
| ENTA | Enanta Pharmaceuticals, Inc. | $14.08 | +10.60% | −2.36% | +62.59% | Nov 16, 2026 |
| 4552.T | JCR Pharmaceuticals Co., Ltd. | 545.00 JPY | +5.21% | −19.79% | −7.40% | Oct 29, 2026 |
| UPB | Upstream Bio, Inc. | $7.18 | +12.19% | −73.48% | −57.08% | Nov 4, 2026 |
| CUV.AX | Clinuvel Pharmaceuticals Limited | 10.54 AUD | +7.44% | −17.07% | −21.84% | Aug 27, 2026 |
| IKT | Inhibikase Therapeutics, Inc. | $2.50 | +6.38% | +28.21% | +42.05% | Nov 13, 2026 |
| PRQR | ProQR Therapeutics N.V. | $2.38 | +37.57% | +19.60% | +5.78% | Nov 5, 2026 |
| TRDA | Entrada Therapeutics, Inc. | $7.62 | +25.33% | −24.18% | +35.35% | Nov 5, 2026 |
| TTRX | Turn Therapeutics Inc. | $9.73 | +25.06% | +107.46% | +39.00% | Nov 12, 2026 |
| FULC | Fulcrum Therapeutics, Inc. | $3.86 | +3.49% | −64.65% | −39.78% | Oct 29, 2026 |
| SION | Sionna Therapeutics, Inc. | $6.25 | −86.23% | −84.06% | −74.02% | Nov 5, 2026 |
| ELDN | Eledon Pharmaceuticals, Inc. | $3.47 | −2.80% | +114.20% | +35.02% | Nov 13, 2026 |
| IVVD | Invivyd, Inc. | $0.94 | +53.89% | −62.45% | +67.62% | Nov 5, 2026 |
| SLGL | Sol-Gel Technologies Ltd. | $81.72 | +2.37% | +93.88% | +289.14% | Nov 19, 2026 |
| XUP.DE | Genfit S.A. | 14.08 EUR | −1.81% | +164.41% | +166.82% | Sep 29, 2026 |
| CRDL | Cardiol Therapeutics Inc. | $2.00 | +73.16% | +101.21% | +75.44% | Nov 12, 2026 |
| CRDL.TO | Cardiol Therapeutics Inc. | 2.76 CAD | +68.29% | +102.94% | +72.50% | Nov 12, 2026 |
| SIGA | SIGA Technologies, Inc. | $3.04 | −1.94% | −45.19% | −60.50% | Nov 5, 2026 |
| ARMP | Armata Pharmaceuticals, Inc. | $5.56 | +7.96% | −15.24% | +113.85% | Nov 11, 2026 |
| MSLE | Satellos Bioscience Inc. | $9.40 | −0.58% | +51.52% | +82.17% | Nov 12, 2026 |
| MSCL.TO | Satellos Bioscience Inc. | 13.00 CAD | −2.26% | +54.76% | +80.56% | Nov 12, 2026 |
| PLX | Protalix BioTherapeutics, Inc. | $2.41 | +0.42% | +38.51% | +50.62% | Nov 12, 2026 |
| 0AB6.L | Hyloris Pharmaceuticals SA | 4.46 EUR | −0.66% | −37.71% | −32.01% | Sep 24, 2026 |
| AARD | Aardvark Therapeutics, Inc. | $7.25 | +8.37% | −45.03% | −19.80% | Nov 12, 2026 |
| MIST | Milestone Pharmaceuticals Inc. | $1.16 | +2.65% | −43.41% | −31.36% | Nov 12, 2026 |
| CPIX | Cumberland Pharmaceuticals Inc. | $8.70 | +59.59% | +118.59% | +166.87% | Nov 3, 2026 |
| INO | Inovio Pharmaceuticals, Inc. | $1.29 | +32.99% | −23.67% | −33.85% | Nov 10, 2026 |
| 0H8T.L | Aclaris Therapeutics, Inc. | $6.58 | +6.50% | +120.68% | +265.21% | Nov 5, 2026 |
| MDP.TO | Medexus Pharmaceuticals Inc. | 5.15 CAD | +3.83% | +66.67% | +80.70% | Nov 11, 2026 |
| RFL | Rafael Holdings, Inc. | $2.24 | −1.75% | +77.78% | +52.38% | Oct 28, 2026 |
| PTHS | Pelthos Therapeutics Inc. | $27.20 | −1.41% | −7.64% | +20.41% | Nov 12, 2026 |
| PYPD | PolyPid Ltd. | $5.10 | +28.14% | +17.24% | +47.83% | Nov 11, 2026 |
Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.