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Rare disease stocks
We cover 92 companies grouped under the Rare disease theme. The median market value in the group is $675.03M. Across the group, the median move over the past trading day is +2.27%. 65% of the 88 with a 200-day average trade above it. Price change over the past year runs from −37.3% to +287.1% across the middle 80 percent of the group, with a median of +49.4%.
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Table
92 of 268 companies match these filters.Clear filters
| Ticker | Company | Price | 1M return | YTD return | 1Y return |
|---|---|---|---|---|---|
| VRTX | Vertex Pharmaceuticals Incorporated | $552.85 | +15.42% | +22.28% | +42.14% |
| ARGX | argenx SE | $1,019.49 | +14.70% | +21.37% | +50.52% |
| ALNY | Alnylam Pharmaceuticals, Inc. | $240.08 | −13.76% | −40.01% | −45.88% |
| INSM | Insmed Incorporated | $123.89 | +18.29% | −30.05% | −3.45% |
| ROIV | Roivant Sciences Ltd. | $36.47 | +5.04% | +66.30% | +213.32% |
| JAZZ | Jazz Pharmaceuticals plc | $260.23 | +1.88% | +50.29% | +108.87% |
| ASND | Ascendis Pharma A/S | $252.99 | −0.17% | +18.61% | +32.89% |
| BBIO | BridgeBio Pharma, Inc. | $80.40 | −4.42% | +2.77% | +70.01% |
| CORT | Corcept Therapeutics Incorporated | $123.57 | +35.61% | +223.48% | +79.56% |
| BMRN | BioMarin Pharmaceutical Inc. | $66.12 | +9.71% | +11.22% | +13.03% |
| ARWR | Arrowhead Pharmaceuticals, Inc. | $88.88 | +3.92% | +31.11% | +329.16% |
| CYTK | Cytokinetics, Incorporated | $77.46 | −3.92% | +25.48% | +109.29% |
| IONS | Ionis Pharmaceuticals, Inc. | $63.57 | +13.60% | −20.21% | +52.01% |
| KYMR | Kymera Therapeutics, Inc. | $126.64 | +15.07% | +74.05% | +202.82% |
| PTGX | Protagonist Therapeutics, Inc. | $150.59 | +11.09% | +72.73% | +164.75% |
| AGIO | Agios Pharmaceuticals, Inc. Common Stock | $33.90 | −8.30% | +24.72% | −9.02% |
| SEPN | Septerna, Inc. | $41.30 | +23.32% | +47.61% | +245.32% |
| ETON | Eton Pharmaceuticals, Inc. | $63.05 | +49.02% | +287.76% | +268.93% |
| ANIP | ANI Pharmaceuticals, Inc. | $75.65 | −3.47% | −3.54% | −16.24% |
| ANAB | AnaptysBio, Inc. | $58.37 | +8.88% | +94.78% | +335.60% |
| AVLN | Avalyn Pharma Inc. | $38.20 | +38.31% | +29.54% | +29.54% |
| MAZE | Maze Therapeutics, Inc. | $30.42 | +6.03% | −23.51% | +128.55% |
| FBRX | Forte Biosciences, Inc. | $76.97 | +0.61% | +226.01% | +580.25% |
| TRAX | First Tracks Biotherapeutics, Inc. | $45.11 | +7.33% | +137.42% | +137.42% |
| XERS | Xeris Biopharma Holdings, Inc. | $8.74 | +6.46% | +18.91% | +12.48% |
| TYRA | Tyra Biosciences, Inc. | $26.69 | −14.07% | −0.37% | +122.42% |
| KALV | KalVista Pharmaceuticals Inc | $27.00 | 0.00% | +74.64% | +107.85% |
| OMER | Omeros Corporation | $19.28 | +70.02% | +17.70% | +343.22% |
| JBIO | Jade Biosciences, Inc. | $21.84 | +9.47% | +54.24% | +176.46% |
| MLTX | MoonLake Immunotherapeutics | $15.56 | −21.73% | +30.21% | −71.52% |
| SVRA | Savara Inc. | $5.60 | +3.13% | −0.71% | +78.34% |
| AVTX | Avalo Therapeutics, Inc. | $19.74 | +1.23% | +15.98% | +110.00% |
| WVE | Wave Life Sciences, Inc. | $5.25 | −11.32% | −67.08% | −47.18% |
| CLYM | Climb Bio Inc | $17.84 | +39.48% | +375.73% | +619.35% |
| DSGN | Design Therapeutics, Inc. | $15.68 | +31.99% | +72.31% | +201.54% |
| ANNX | Annexon, Inc. | $5.15 | +0.39% | +9.81% | +139.53% |
| DBVT | DBV Technologies S.A. | $14.97 | +7.70% | −21.42% | +52.91% |
| SLN | Silence Therapeutics plc | $13.67 | +13.26% | +122.28% | +170.16% |
| PHAR | Pharming Group N.V. | $11.46 | −11.93% | −33.14% | −19.75% |
| STTK | Shattuck Labs, Inc. | $8.06 | +14.49% | +117.25% | +710.87% |
| TECX | Tectonic Therapeutic, Inc. | $37.71 | +23.20% | +80.34% | +53.48% |
| IRWD | Ironwood Pharmaceuticals, Inc. | $4.39 | +12.28% | +2.81% | +245.67% |
| ASMB | Assembly Biosciences, Inc. | $35.33 | +36.36% | +4.68% | +32.72% |
| ZVRA | Zevra Therapeutics, Inc. | $12.04 | +24.00% | +44.36% | +28.63% |
| AGMB | AgomAb Therapeutics NV | $14.02 | +12.07% | −4.30% | −4.30% |
| GYRE | Gyre Therapeutics, Inc. | $6.68 | +8.97% | −1.91% | −18.54% |
| CRMD | CorMedix Inc. | $8.56 | +12.63% | −29.61% | −37.65% |
| VALN | Valneva SE | $6.78 | +36.69% | −24.29% | −28.10% |
| ZURA | Zura Bio Limited | $6.32 | +17.47% | +13.87% | +208.29% |
| AQST | Aquestive Therapeutics, Inc. | $5.08 | +36.19% | −21.24% | +31.61% |
| SPRY | ARS Pharmaceuticals, Inc. | $5.72 | −0.69% | −50.22% | −57.66% |
| KMDA | Kamada Ltd. Ordinary Shares | $8.63 | +23.46% | +26.48% | +26.12% |
| EPRX | Eupraxia Pharmaceuticals Inc. | $7.42 | +20.26% | −1.98% | +41.87% |
| QTTB | Q32 Bio Inc. | $16.32 | +7.30% | +374.42% | +728.43% |
| RZLT | Rezolute, Inc. | $5.01 | +1.42% | +131.41% | −28.43% |
| AVIR | Atea Pharmaceuticals, Inc. | $5.43 | +12.66% | +56.03% | +48.36% |
| LRMR | Larimar Therapeutics, Inc. | $4.16 | +8.62% | +19.88% | +11.83% |
| XFOR | X4 Pharmaceuticals, Inc. | $4.16 | +5.58% | +6.94% | +4.79% |
| ENTA | Enanta Pharmaceuticals, Inc. | $14.08 | +10.60% | −2.36% | +62.59% |
| UPB | Upstream Bio, Inc. | $7.18 | +12.19% | −73.48% | −57.08% |
| IKT | Inhibikase Therapeutics, Inc. | $2.50 | +6.38% | +28.21% | +42.05% |
| PRQR | ProQR Therapeutics N.V. | $2.38 | +37.57% | +19.60% | +5.78% |
| IFRX | InflaRx N.V. | $2.46 | +44.71% | +125.69% | +167.10% |
| TRDA | Entrada Therapeutics, Inc. | $7.62 | +25.33% | −24.18% | +35.35% |
| TTRX | Turn Therapeutics Inc. | $9.73 | +25.06% | +107.46% | +39.00% |
| FULC | Fulcrum Therapeutics, Inc. | $3.86 | +3.49% | −64.65% | −39.78% |
| SION | Sionna Therapeutics, Inc. | $6.25 | −86.23% | −84.06% | −74.02% |
| ELDN | Eledon Pharmaceuticals, Inc. | $3.47 | −2.80% | +114.20% | +35.02% |
| CAMP | CAMP4 THERAPEUTICS CORPORATION | $4.45 | +30.12% | −25.83% | +185.26% |
| IVVD | Invivyd, Inc. | $0.94 | +53.89% | −62.45% | +67.62% |
| AKBA | Akebia Therapeutics, Inc. | $0.96 | −25.12% | −38.17% | −68.37% |
| SLGL | Sol-Gel Technologies Ltd. | $81.72 | +2.37% | +93.88% | +289.14% |
| RNA | Prosensa Holding B.V. Ordinary Shares | $14.00 | +21.00% | −5.08% | −5.08% |
| PEPG | PepGen Inc. | $3.43 | +80.26% | −52.23% | +161.45% |
| CRDL | Cardiol Therapeutics Inc. | $2.00 | +73.16% | +101.21% | +75.44% |
| KROS | Keros Therapeutics, Inc. | $11.68 | +14.40% | −37.00% | −20.87% |
| ANTX | AN2 Therapeutics, Inc. | $5.66 | +14.81% | +409.91% | +403.11% |
| SIGA | SIGA Technologies, Inc. | $3.04 | −1.94% | −45.19% | −60.50% |
| ARMP | Armata Pharmaceuticals, Inc. | $5.56 | +7.96% | −15.24% | +113.85% |
| MSLE | Satellos Bioscience Inc. | $9.40 | −0.58% | +51.52% | +82.17% |
| PLX | Protalix BioTherapeutics, Inc. | $2.41 | +0.42% | +38.51% | +50.62% |
| SPRB | Spruce Biosciences, Inc. | $63.40 | +50.99% | −30.10% | +697.48% |
| MDWD | MediWound Ltd. | $12.97 | −10.24% | −29.59% | −24.81% |
| AARD | Aardvark Therapeutics, Inc. | $7.25 | +8.37% | −45.03% | −19.80% |
| UNCY | Unicycive Therapeutics, Inc. | $5.47 | +6.63% | −5.69% | +27.51% |
| MIST | Milestone Pharmaceuticals Inc. | $1.16 | +2.65% | −43.41% | −31.36% |
| EQ | Equillium, Inc. | $2.18 | −11.38% | +42.48% | +14.74% |
| CPIX | Cumberland Pharmaceuticals Inc. | $8.70 | +59.59% | +118.59% | +166.87% |
| INO | Inovio Pharmaceuticals, Inc. | $1.29 | +32.99% | −23.67% | −33.85% |
| RFL | Rafael Holdings, Inc. | $2.24 | −1.75% | +77.78% | +52.38% |
| PTHS | Pelthos Therapeutics Inc. | $27.20 | −1.41% | −7.64% | +20.41% |
| PYPD | PolyPid Ltd. | $5.10 | +28.14% | +17.24% | +47.83% |
Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.