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Rare disease stocks
We cover 17 companies grouped under the Rare disease theme. The median market value in the group is $12.95B. Across the group, the median move over the past trading day is −0.26%. Price change over the past year runs from −8.6% to +200.9% across the middle 80 percent of the group, with a median of +48.2%.
Other lists in this group
SaaSAI applicationsCybersecuritySemiconductor designSemiconductor equipmentFintech softwarePayment processingEcommerce marketplacesStreaming mediaGaming softwareOncologyRare diseaseMedical devicesCell therapyDiagnosticsRegional banksAsset managementGold miningCryptocurrency and digital assetsSpecialty chemicalsAll stocks
Table
17 of 268 companies match these filters.Clear filters
| Ticker | Company | Market cap (USD) | Size | 1Y return | Next report |
|---|---|---|---|---|---|
| VX1.DE | Vertex Pharmaceuticals Incorporated | $139.82B | Large cap | +41.64% | Nov 2, 2026 |
| VRTX | Vertex Pharmaceuticals Incorporated | $138.63B | Large cap | +40.66% | Nov 2, 2026 |
| DUL.DE | Alnylam Pharmaceuticals, Inc. | $32.28B | Large cap | −10.21% | Oct 29, 2026 |
| ALNY | Alnylam Pharmaceuticals, Inc. | $32.12B | Large cap | −47.38% | Oct 29, 2026 |
| INSM | Insmed Incorporated | $27.16B | Large cap | −7.54% | Oct 29, 2026 |
| ROIV | Roivant Sciences Ltd. | $26.55B | Large cap | +206.51% | Nov 9, 2026 |
| JAZZ | Jazz Pharmaceuticals plc | $16.89B | Large cap | +100.35% | Nov 4, 2026 |
| BBIO | BridgeBio Pharma, Inc. | $15.52B | Large cap | +60.05% | Oct 28, 2026 |
| CORT | Corcept Therapeutics Incorporated | $12.95B | Large cap | +71.81% | Nov 4, 2026 |
| 0JAV.L | Insmed Incorporated | $12.89B | Large cap | −7.52% | Oct 29, 2026 |
| BMRN | BioMarin Pharmaceutical Inc. | $12.70B | Large cap | +11.85% | Oct 26, 2026 |
| REC.MI | Recordati Industria Chimica e Farmaceutica S.p.A. | $12.57B | Large cap | +1.80% | Nov 10, 2026 |
| ARWR | Arrowhead Pharmaceuticals, Inc. | $12.52B | Large cap | +308.99% | Nov 24, 2026 |
| CYTK | Cytokinetics, Incorporated | $11.01B | Large cap | +109.36% | Nov 5, 2026 |
| IONS | Ionis Pharmaceuticals, Inc. | $10.56B | Large cap | +48.21% | Nov 4, 2026 |
| KYMR | Kymera Therapeutics, Inc. | $10.53B | Large cap | +197.09% | Nov 3, 2026 |
| ABVX.PA | ABIVAX Société Anonyme | $10.21B | Large cap | +48.91% | Sep 21, 2026 |
Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.