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Rare disease stocks
We cover 31 companies grouped under the Rare disease theme. The median market value in the group is $10.53B. Across the group, the median move over the past trading day is −0.61%. 50% of the 30 with a 200-day average trade above it. Price change over the past year runs from −89.3% to +197.1% across the middle 80 percent of the group, with a median of +1.8%.
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SaaSAI applicationsCybersecuritySemiconductor designSemiconductor equipmentFintech softwarePayment processingEcommerce marketplacesStreaming mediaGaming softwareOncologyRare diseaseMedical devicesCell therapyDiagnosticsRegional banksAsset managementGold miningCryptocurrency and digital assetsSpecialty chemicalsAll stocks
Table
31 of 268 companies match these filters.Clear filters
| Ticker | Company | Market cap (USD) | Size | 1Y return | Next report |
|---|---|---|---|---|---|
| VX1.DE | Vertex Pharmaceuticals Incorporated | $139.82B | Large cap | +41.64% | Nov 2, 2026 |
| VRTX | Vertex Pharmaceuticals Incorporated | $138.63B | Large cap | +40.66% | Nov 2, 2026 |
| ARGX | argenx SE | $65.51B | Large cap | +47.90% | Oct 22, 2026 |
| DUL.DE | Alnylam Pharmaceuticals, Inc. | $32.28B | Large cap | −10.21% | Oct 29, 2026 |
| ALNY | Alnylam Pharmaceuticals, Inc. | $32.12B | Large cap | −47.38% | Oct 29, 2026 |
| INSM | Insmed Incorporated | $27.16B | Large cap | −7.54% | Oct 29, 2026 |
| ROIV | Roivant Sciences Ltd. | $26.55B | Large cap | +206.51% | Nov 9, 2026 |
| JAZZ | Jazz Pharmaceuticals plc | $16.89B | Large cap | +100.35% | Nov 4, 2026 |
| BBIO | BridgeBio Pharma, Inc. | $15.52B | Large cap | +60.05% | Oct 28, 2026 |
| CORT | Corcept Therapeutics Incorporated | $12.95B | Large cap | +71.81% | Nov 4, 2026 |
| BMRN | BioMarin Pharmaceutical Inc. | $12.70B | Large cap | +11.85% | Oct 26, 2026 |
| REC.MI | Recordati Industria Chimica e Farmaceutica S.p.A. | $12.57B | Large cap | +1.80% | Nov 10, 2026 |
| ARWR | Arrowhead Pharmaceuticals, Inc. | $12.52B | Large cap | +308.99% | Nov 24, 2026 |
| CYTK | Cytokinetics, Incorporated | $11.01B | Large cap | +109.36% | Nov 5, 2026 |
| IONS | Ionis Pharmaceuticals, Inc. | $10.56B | Large cap | +48.21% | Nov 4, 2026 |
| KYMR | Kymera Therapeutics, Inc. | $10.53B | Large cap | +197.09% | Nov 3, 2026 |
| ABVX.PA | ABIVAX Société Anonyme | $10.21B | Large cap | +48.91% | Sep 21, 2026 |
| GOSS | Gossamer Bio, Inc. | $85.01M | Micro cap | −92.93% | Nov 4, 2026 |
| SPRO | Spero Therapeutics, Inc. | $71.05M | Micro cap | −38.38% | Nov 12, 2026 |
| SCYX | SCYNEXIS, Inc. | $56.41M | Micro cap | +579.04% | Nov 4, 2026 |
| ATYR | aTyr Pharma, Inc. | $54.05M | Micro cap | −89.34% | Nov 5, 2026 |
| MCRB | Seres Therapeutics, Inc. | $47.81M | Micro cap | −74.79% | Nov 4, 2026 |
| MREO | Mereo BioPharma Group plc | $44.39M | Micro cap | −84.20% | Nov 9, 2026 |
| QNCX | Quince Therapeutics, Inc. | $31.84M | Micro cap | +100.71% | Nov 12, 2026 |
| RVX.TO | Resverlogix Corp. | $24.81M | Micro cap | 0.00% | Nov 12, 2026 |
| JSPR | Jasper Therapeutics, Inc. | $23.96M | Micro cap | −75.24% | Nov 10, 2026 |
| TVRD | Tvardi Therapeutics, Inc. | $23.74M | Micro cap | −94.18% | Nov 12, 2026 |
| INM | InMed Pharmaceuticals Inc. | $7.64M | Micro cap | −36.44% | Sep 23, 2026 |
| JAGX | Jaguar Health, Inc. | $4.78M | Micro cap | −98.52% | Nov 12, 2026 |
| XRTX | XORTX Therapeutics Inc. | $4.03M | Micro cap | −43.99% | Nov 12, 2026 |
| APLI.TO | Appili Therapeutics Inc. | $1.44M | Micro cap | −25.00% | Nov 12, 2026 |
Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.