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Rare disease stocks
We cover 99 companies grouped under the Rare disease theme. The median market value in the group is $46.28M. Across the group, the median move over the past trading day is +0.69%. 39% of the 95 with a 200-day average trade above it. Price change over the past year runs from −87.2% to +109.0% across the middle 80 percent of the group, with a median of −22.4%.
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Table
99 of 268 companies match these filters.Clear filters
| Ticker | Company | Price | 1M return | YTD return | 1Y return |
|---|---|---|---|---|---|
| VX1.DE | Vertex Pharmaceuticals Incorporated | 469.95 EUR | +10.56% | +22.24% | +40.14% |
| VRTX34.SA | Vertex Pharmaceuticals Incorporated | 88.83 BRL | +19.14% | −85.56% | −83.17% |
| VRTX | Vertex Pharmaceuticals Incorporated | $552.85 | +15.42% | +22.28% | +42.14% |
| 0QZU.L | Vertex Pharmaceuticals Incorporated | $554.44 | +1.12% | +23.31% | +42.39% |
| ARGX | argenx SE | $1,019.49 | +14.70% | +21.37% | +50.52% |
| A1RG34.SA | argenx SE | 209.16 BRL | +18.17% | +11.37% | +44.49% |
| 0HD2.L | Alnylam Pharmaceuticals, Inc. | $240.20 | −4.67% | −39.64% | −46.85% |
| ALNY | Alnylam Pharmaceuticals, Inc. | $240.08 | −13.76% | −40.01% | −45.88% |
| DUL.DE | Alnylam Pharmaceuticals, Inc. | 200.50 EUR | −20.91% | −41.22% | −11.75% |
| A1LN34.SA | Alnylam Pharmaceuticals, Inc. | 61.14 BRL | −11.65% | −45.14% | −49.89% |
| INSM | Insmed Incorporated | $123.89 | +18.29% | −30.05% | −3.45% |
| ROIV | Roivant Sciences Ltd. | $36.47 | +5.04% | +66.30% | +213.32% |
| JAZZ | Jazz Pharmaceuticals plc | $260.23 | +1.88% | +50.29% | +108.87% |
| ASND | Ascendis Pharma A/S | $252.99 | −0.17% | +18.61% | +32.89% |
| BBIO | BridgeBio Pharma, Inc. | $80.40 | −4.42% | +2.77% | +70.01% |
| CORT | Corcept Therapeutics Incorporated | $123.57 | +35.61% | +223.48% | +79.56% |
| 0JAV.L | Insmed Incorporated | $125.32 | +0.69% | −28.09% | −6.25% |
| BMRN | BioMarin Pharmaceutical Inc. | $66.12 | +9.71% | +11.22% | +13.03% |
| REC.MI | Recordati Industria Chimica e Farmaceutica S.p.A. | 52.70 EUR | +2.73% | +10.68% | +2.09% |
| B1MR34.SA | BioMarin Pharmaceutical Inc. | 166.77 BRL | +12.08% | −0.14% | +6.36% |
| ARWR | Arrowhead Pharmaceuticals, Inc. | $88.88 | +3.92% | +31.11% | +329.16% |
| CYTK | Cytokinetics, Incorporated | $77.46 | −3.92% | +25.48% | +109.29% |
| IONS | Ionis Pharmaceuticals, Inc. | $63.57 | +13.60% | −20.21% | +52.01% |
| KYMR | Kymera Therapeutics, Inc. | $126.64 | +15.07% | +74.05% | +202.82% |
| ABVX.PA | ABIVAX Société Anonyme | 98.10 EUR | −9.83% | −14.70% | +42.59% |
| 0JDI.L | Ionis Pharmaceuticals, Inc. | $63.80 | +4.15% | −19.18% | +49.07% |
| PTGX | Protagonist Therapeutics, Inc. | $150.59 | +11.09% | +72.73% | +164.75% |
| GOSS | Gossamer Bio, Inc. | $0.20 | +2.76% | −92.90% | −91.33% |
| ILA.AX | Island Pharmaceuticals Limited | 0.47 AUD | +20.51% | +8.05% | +104.35% |
| ABNX.PA | ABIONYX Pharma SA | 1.94 EUR | +1.25% | −50.45% | −16.20% |
| PAR.AX | Paradigm Biopharmaceuticals Limited | 0.23 AUD | +36.36% | −33.82% | −22.41% |
| 0RAG.L | ABIONYX Pharma SA | 1.97 EUR | +1.34% | −49.42% | −18.26% |
| FBIO | Fortress Biotech, Inc. | $2.83 | −13.46% | −29.78% | +23.58% |
| PLYX | Polaryx Therapeutics, Inc. | $1.87 | −4.59% | −94.66% | −94.66% |
| RLYB | Rallybio Corporation | $16.89 | +3.53% | +198.53% | +262.65% |
| TENX | Tenax Therapeutics, Inc. | $2.32 | −85.67% | −79.00% | −60.81% |
| TELO | Telomir Pharmaceuticals, Inc. | $1.18 | −4.07% | −11.94% | −19.18% |
| RCE.AX | Recce Pharmaceuticals Ltd | 0.38 AUD | +2.74% | −43.82% | −12.79% |
| FBIOP | Fortress Biotech, Inc. | $18.30 | −2.66% | +80.12% | +141.55% |
| STX.L | Shield Therapeutics plc | 4.70 GBP | −18.97% | −52.28% | −41.98% |
| SPRO | Spero Therapeutics, Inc. | $1.23 | +4.24% | −47.66% | −33.51% |
| ALTHX.PA | THX Pharma Société Anonyme | 4.09 EUR | +3.81% | +80.18% | +89.35% |
| RNTX | Rein Therapeutics Inc. | $0.80 | +2.30% | −36.00% | −32.20% |
| IMA | ImageneBio, Inc. | $5.55 | −0.89% | −17.90% | −60.78% |
| 0IIM.L | Esperion Therapeutics, Inc. | $3.19 | +0.14% | −14.28% | +46.64% |
| ATYR | aTyr Pharma, Inc. | $0.57 | +16.33% | −24.90% | −88.95% |
| SCYX | SCYNEXIS, Inc. | $5.19 | +45.38% | +712.21% | +514.20% |
| NSRX | Nasus Pharma Ltd. | $4.10 | +32.69% | −45.70% | −48.69% |
| MCRB | Seres Therapeutics, Inc. | $5.00 | +3.09% | −67.00% | −74.00% |
| GRCE | Grace Therapeutics, Inc. | $2.20 | −4.35% | −39.89% | −32.31% |
| MREO | Mereo BioPharma Group plc | $0.28 | −6.75% | −44.78% | −83.82% |
| EDSA | Edesa Biotech, Inc. | $4.45 | −16.82% | +196.67% | +83.88% |
| BOT.AX | Botanix Pharmaceuticals Limited | 0.02 AUD | −4.76% | −85.19% | −87.10% |
| QNCX | Quince Therapeutics, Inc. | $30.93 | +73.28% | +3.10% | +95.76% |
| NNVC | NanoViricides, Inc. | $1.29 | −16.23% | +6.61% | −12.84% |
| 520A.T | J-PHARMACEUTICALS CO LTD | 275.00 JPY | −0.72% | −60.71% | −60.71% |
| ALDVI.PA | Advicenne S.A. | 1.73 EUR | +8.37% | −6.87% | +41.44% |
| 4591.T | Ribomic Inc. | 84.00 JPY | +18.31% | +7.69% | −22.94% |
| IMM.L | ImmuPharma plc | 3.41 GBP | −24.33% | −45.08% | +83.56% |
| 0RQJ.L | Saniona AB (publ) | 11.75 SEK | +0.04% | −44.31% | −13.86% |
| BRNS | Barinthus Biotherapeutics plc | $0.66 | +9.82% | −10.20% | −44.77% |
| JSPR | Jasper Therapeutics, Inc. | $0.72 | +3.78% | −60.86% | −75.67% |
| TVRD | Tvardi Therapeutics, Inc. | $1.82 | −28.35% | −55.39% | −93.77% |
| RVX.TO | Resverlogix Corp. | 0.11 CAD | −4.55% | +5.00% | +5.00% |
| 4884.T | Kringle Pharma, Inc. | 450.00 JPY | +44.23% | +14.80% | −7.41% |
| COCP | Cocrystal Pharma, Inc. | $1.13 | +22.83% | +14.14% | −26.62% |
| VYNE | VYNE Therapeutics Inc | $28.56 | +3080.40% | +4824.14% | +8687.69% |
| KTTA | Pasithea Therapeutics Corp. | $0.56 | +24.44% | −52.94% | −21.90% |
| CALC | CalciMedica, Inc. | $0.59 | −16.36% | −91.28% | −78.92% |
| CMMB | Chemomab Therapeutics Ltd. | $2.30 | +61.97% | +28.49% | −33.91% |
| 4881.T | FunPep Company Limited | 50.00 JPY | −3.85% | −38.27% | −56.14% |
| HIND | Vyome Holdings, Inc. | $2.23 | +11.50% | −37.18% | −80.23% |
| ALBPS.PA | Biophytis S.A. | 0.08 EUR | +417.65% | +27.13% | −53.47% |
| ANNX.ST | Annexin Pharmaceuticals AB (publ) | 13.20 SEK | +5.60% | −33.67% | −49.23% |
| QNRX | Quoin Pharmaceuticals, Ltd. | $5.07 | +18.18% | −63.99% | −31.02% |
| AZTR | Azitra, Inc. | $0.16 | +23.05% | −43.55% | −78.97% |
| PHR.WA | Pharmena S.A. | 3.20 PLN | +3.56% | +20.75% | −7.51% |
| IMRN | Immuron Limited | $1.14 | +7.55% | +43.40% | −36.84% |
| SNGX | Soligenix, Inc. | $0.41 | +12.53% | −71.47% | −87.06% |
| IMC.AX | Immuron Limited | 0.04 AUD | 0.00% | +5.71% | −46.38% |
| XCUR | Exicure, Inc. | $1.19 | −32.00% | −78.67% | −79.90% |
| INM | InMed Pharmaceuticals Inc. | $1.44 | −12.20% | +28.57% | −35.43% |
| VBS.AX | Vectus Biosystems Limited | 0.15 AUD | 0.00% | −9.09% | +87.50% |
| PULM | Pulmatrix, Inc. | $1.60 | −7.51% | −29.20% | −67.81% |
| BIOSGN.ST | Biosergen AB (publ) | 2.30 SEK | +236.01% | −94.25% | −95.33% |
| JAGX | Jaguar Health, Inc. | $0.92 | −7.51% | −97.35% | −98.52% |
| CVKD | Cadrenal Therapeutics, Inc. | $1.53 | −25.73% | −79.13% | −87.58% |
| GLMD | Galmed Pharmaceuticals Ltd. | $4.31 | +716.94% | +423.12% | +205.34% |
| GRI | GRI Bio, Inc. | $1.96 | +40.00% | −75.00% | −95.14% |
| XRTX | XORTX Therapeutics Inc. | $2.26 | +11.88% | −20.70% | −44.74% |
| BIT.AX | Biotron Limited | 0.00 AUD | 0.00% | −42.86% | −33.33% |
| SXTP | 60 Degrees Pharmaceuticals, Inc. | $1.13 | −28.03% | −45.25% | −78.10% |
| MTNB | Matinas BioPharma Holdings, Inc. | $0.20 | −40.57% | −68.18% | −90.82% |
| ANR.AX | Anatara Lifesciences Ltd | 0.01 AUD | −10.00% | −35.71% | +12.50% |
| APTA.ST | Aptahem AB (publ) | 0.51 SEK | −24.25% | −56.19% | −72.50% |
| APLI.TO | Appili Therapeutics Inc. | 0.02 CAD | +50.00% | −40.00% | −25.00% |
| VBIO | Valion Bio, Inc. | $0.16 | −43.82% | −88.80% | −95.00% |
| 0R55.L | BioSenic S.A. | 0.00 EUR | 0.00% | −4.76% | −23.08% |
| ALNEV.PA | Neovacs S.A. | 0.61 EUR | −21.73% | +6834.09% | −11.54% |
Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.