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Rare disease stocks
We cover 18 companies grouped under the Rare disease theme. The median market value in the group is $1.55B. Across the group, the median move over the past trading day is −0.42%. Price change over the past year runs from −37.6% to +251.2% across the middle 80 percent of the group, with a median of +28.1%.
Other lists in this group
SaaSAI applicationsCybersecuritySemiconductor designSemiconductor equipmentFintech softwarePayment processingEcommerce marketplacesStreaming mediaGaming softwareOncologyRare diseaseMedical devicesCell therapyDiagnosticsRegional banksAsset managementGold miningCryptocurrency and digital assetsSpecialty chemicalsAll stocks
Table
18 of 268 companies match these filters.Clear filters
| Ticker | Company | Market cap (USD) | Size | 1Y return | Next report |
|---|---|---|---|---|---|
| VX1.DE | Vertex Pharmaceuticals Incorporated | $139.26B | Large cap | +41.04% | Nov 2, 2026 |
| 0QZU.L | Vertex Pharmaceuticals Incorporated | $112.52B | Large cap | +37.72% | Nov 2, 2026 |
| 0HD2.L | Alnylam Pharmaceuticals, Inc. | $35.05B | Large cap | −47.73% | Oct 29, 2026 |
| DUL.DE | Alnylam Pharmaceuticals, Inc. | $31.11B | Large cap | −8.93% | Oct 29, 2026 |
| 0JAV.L | Insmed Incorporated | $12.89B | Large cap | −9.79% | Oct 29, 2026 |
| REC.MI | Recordati Industria Chimica e Farmaceutica S.p.A. | $12.56B | Large cap | +2.58% | Nov 10, 2026 |
| 0JDI.L | Ionis Pharmaceuticals, Inc. | $10.40B | Large cap | +48.29% | Nov 4, 2026 |
| ABVX.PA | ABIVAX Société Anonyme | $10.07B | Large cap | +46.14% | Sep 21, 2026 |
| 0L35.L | Sarepta Therapeutics, Inc. | $1.69B | Small cap | +18.56% | Nov 4, 2026 |
| 0LIF.L | Ultragenyx Pharmaceutical Inc. | $1.40B | Small cap | −13.32% | Nov 3, 2026 |
| 0HB0.L | Agios Pharmaceuticals, Inc. | $1.19B | Small cap | −7.83% | Oct 29, 2026 |
| DBV.PA | DBV Technologies S.A. | $923.84M | Small cap | +56.64% | Oct 28, 2026 |
| GNFT.PA | Genfit S.A. | $870.63M | Small cap | +327.25% | Sep 29, 2026 |
| 0KBU.L | Omeros Corporation | $575.28M | Small cap | +372.12% | Nov 12, 2026 |
| XUP.DE | Genfit S.A. | $258.22M | Small cap | +166.82% | Sep 29, 2026 |
| 0AB6.L | Hyloris Pharmaceuticals SA | $185.32M | Small cap | −33.23% | Sep 24, 2026 |
| CRNO-B.ST | Cereno Scientific AB (publ) | $148.07M | Small cap | −54.67% | Nov 4, 2026 |
| 0H8T.L | Aclaris Therapeutics, Inc. | $122.82M | Small cap | +218.56% | Nov 5, 2026 |
Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.