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Rare disease stocks
We cover 15 companies grouped under the Rare disease theme. The median market value in the group is $27.07B. Across the group, the median move over the past trading day is +0.48%. Price change over the past year runs from −32.2% to +142.6% across the middle 80 percent of the group, with a median of +42.1%.
Other lists in this group
SaaSAI applicationsCybersecuritySemiconductor designSemiconductor equipmentFintech softwarePayment processingEcommerce marketplacesStreaming mediaGaming softwareOncologyRare diseaseMedical devicesCell therapyDiagnosticsRegional banksAsset managementGold miningCryptocurrency and digital assetsSpecialty chemicalsAll stocks
Table
15 of 268 companies match these filters.Clear filters
| Ticker | Company | Market cap (USD) | Size | 1Y return | Next report |
|---|---|---|---|---|---|
| VX1.DE | Vertex Pharmaceuticals Incorporated | $140.77B | Large cap | +40.14% | Nov 2, 2026 |
| VRTX | Vertex Pharmaceuticals Incorporated | $140.04B | Large cap | +42.14% | Nov 2, 2026 |
| 0QZU.L | Vertex Pharmaceuticals Incorporated | $112.52B | Large cap | +42.39% | Nov 2, 2026 |
| ARGX | argenx SE | $63.78B | Large cap | +50.52% | Oct 22, 2026 |
| 0HD2.L | Alnylam Pharmaceuticals, Inc. | $35.05B | Large cap | −46.85% | Oct 29, 2026 |
| ALNY | Alnylam Pharmaceuticals, Inc. | $32.12B | Large cap | −45.88% | Oct 29, 2026 |
| DUL.DE | Alnylam Pharmaceuticals, Inc. | $31.87B | Large cap | −11.75% | Oct 29, 2026 |
| INSM | Insmed Incorporated | $27.07B | Large cap | −3.45% | Oct 29, 2026 |
| BBIO | BridgeBio Pharma, Inc. | $15.85B | Large cap | +70.01% | Oct 28, 2026 |
| 0JAV.L | Insmed Incorporated | $12.89B | Large cap | −6.25% | Oct 29, 2026 |
| BMRN | BioMarin Pharmaceutical Inc. | $12.80B | Large cap | +13.03% | Oct 26, 2026 |
| CYTK | Cytokinetics, Incorporated | $10.77B | Large cap | +109.29% | Nov 5, 2026 |
| KYMR | Kymera Therapeutics, Inc. | $10.53B | Large cap | +202.82% | Nov 3, 2026 |
| ABVX.PA | ABIVAX Société Anonyme | $10.42B | Large cap | +42.59% | Sep 21, 2026 |
| PTGX | Protagonist Therapeutics, Inc. | $10.01B | Large cap | +164.75% | Nov 5, 2026 |
Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.