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Rare disease stocks

We cover 20 companies grouped under the Rare disease theme. The median market value in the group is $14.23B. Across the group, the median move over the past trading day is −0.30%. Price change over the past year runs from −13.9% to +198.0% across the middle 80 percent of the group, with a median of +44.5%.

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Table

20 of 268 companies match these filters.Clear filters

TickerCompanyMarket cap (USD)Size1Y return
VX1.DEVertex Pharmaceuticals Incorporated$139.82BLarge cap+41.64%
VRTXVertex Pharmaceuticals Incorporated$138.63BLarge cap+40.66%
DUL.DEAlnylam Pharmaceuticals, Inc.$32.28BLarge cap−10.21%
ALNYAlnylam Pharmaceuticals, Inc.$32.12BLarge cap−47.38%
A1LN34.SAAlnylam Pharmaceuticals, Inc.$31.78BLarge cap−49.35%
INSMInsmed Incorporated$27.16BLarge cap−7.54%
ROIVRoivant Sciences Ltd.$26.55BLarge cap+206.51%
JAZZJazz Pharmaceuticals plc$16.89BLarge cap+100.35%
ASNDAscendis Pharma A/S$16.41BLarge cap+29.66%
BBIOBridgeBio Pharma, Inc.$15.52BLarge cap+60.05%
CORTCorcept Therapeutics Incorporated$12.95BLarge cap+71.81%
0JAV.LInsmed Incorporated$12.89BLarge cap−7.52%
BMRNBioMarin Pharmaceutical Inc.$12.70BLarge cap+11.85%
REC.MIRecordati Industria Chimica e Farmaceutica S.p.A.$12.57BLarge cap+1.80%
ARWRArrowhead Pharmaceuticals, Inc.$12.52BLarge cap+308.99%
CYTKCytokinetics, Incorporated$11.01BLarge cap+109.36%
IONSIonis Pharmaceuticals, Inc.$10.56BLarge cap+48.21%
KYMRKymera Therapeutics, Inc.$10.53BLarge cap+197.09%
0JDI.LIonis Pharmaceuticals, Inc.$10.40BLarge cap+47.26%
ABVX.PAABIVAX Société Anonyme$10.21BLarge cap+48.91%

Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.

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