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Rare disease stocks
We cover 62 companies grouped under the Rare disease theme. The median market value in the group is $462.70M. Across the group, the median move over the past trading day is −1.15%. 62% of the 60 with a 200-day average trade above it. Price change over the past year runs from −48.0% to +216.4% across the middle 80 percent of the group, with a median of +39.6%.
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Table
62 of 268 companies match these filters.Clear filters
| Ticker | Company | Market cap (USD) | Size | 1Y return | Next report |
|---|---|---|---|---|---|
| SEPN | Septerna, Inc. | $1.88B | Small cap | +218.81% | Nov 9, 2026 |
| ETON | Eton Pharmaceuticals, Inc. | $1.79B | Small cap | +262.38% | Nov 12, 2026 |
| ANIP | ANI Pharmaceuticals, Inc. | $1.71B | Small cap | −18.85% | Nov 6, 2026 |
| MAZE | Maze Therapeutics, Inc. | $1.69B | Small cap | +113.27% | Nov 5, 2026 |
| AVLN | Avalyn Pharma Inc. | $1.64B | Small cap | +25.60% | Nov 16, 2026 |
| FBRX | Forte Biosciences, Inc. | $1.63B | Small cap | +589.87% | Nov 9, 2026 |
| XERS | Xeris Biopharma Holdings, Inc. | $1.58B | Small cap | +8.64% | Nov 5, 2026 |
| TRAX | First Tracks Biotherapeutics, Inc. | $1.58B | Small cap | +132.58% | Nov 5, 2026 |
| TYRA | Tyra Biosciences, Inc. | $1.56B | Small cap | +103.57% | Nov 4, 2026 |
| OMER | Omeros Corporation | $1.40B | Small cap | +328.71% | Nov 12, 2026 |
| JBIO | Jade Biosciences, Inc. | $1.39B | Small cap | +168.30% | Nov 12, 2026 |
| MLTX | MoonLake Immunotherapeutics | $1.32B | Small cap | −71.82% | Nov 5, 2026 |
| SVRA | Savara Inc. | $1.15B | Small cap | +70.52% | Nov 11, 2026 |
| AVTX | Avalo Therapeutics, Inc. | $1.10B | Small cap | +112.95% | Nov 12, 2026 |
| WVE | Wave Life Sciences, Inc. | $1.03B | Small cap | −48.12% | Nov 9, 2026 |
| DSGN | Design Therapeutics, Inc. | $975.65M | Small cap | +194.71% | Nov 5, 2026 |
| ANNX | Annexon, Inc. | $946.00M | Small cap | +136.49% | Nov 9, 2026 |
| DBVT | DBV Technologies S.A. | $940.80M | Small cap | +53.00% | Oct 28, 2026 |
| SLN | Silence Therapeutics plc | $840.94M | Small cap | +160.19% | Nov 5, 2026 |
| STTK | Shattuck Labs, Inc. | $792.87M | Small cap | +690.00% | Nov 12, 2026 |
| IRWD | Ironwood Pharmaceuticals, Inc. | $708.88M | Small cap | +240.48% | Nov 9, 2026 |
| GYRE | Gyre Therapeutics, Inc. | $705.12M | Small cap | −18.00% | Nov 5, 2026 |
| TECX | Tectonic Therapeutic, Inc. | $703.19M | Small cap | +35.43% | Nov 5, 2026 |
| ZVRA | Zevra Therapeutics, Inc. | $697.17M | Small cap | +25.43% | Nov 4, 2026 |
| AQST | Aquestive Therapeutics, Inc. | $676.51M | Small cap | +40.00% | Nov 4, 2026 |
| CRMD | CorMedix Inc. | $653.95M | Small cap | −40.66% | Nov 16, 2026 |
| ZURA | Zura Bio Limited | $574.02M | Small cap | +177.31% | Nov 12, 2026 |
| SPRY | ARS Pharmaceuticals, Inc. | $568.84M | Small cap | −55.13% | Nov 10, 2026 |
| EPRX | Eupraxia Pharmaceuticals Inc. | $490.26M | Small cap | +40.72% | Nov 3, 2026 |
| RZLT | Rezolute, Inc. | $485.31M | Small cap | −30.00% | Sep 16, 2026 |
| KMDA | Kamada Ltd. Ordinary Shares | $483.48M | Small cap | +21.09% | Nov 9, 2026 |
| AVIR | Atea Pharmaceuticals, Inc. | $441.93M | Small cap | +53.06% | Nov 11, 2026 |
| LRMR | Larimar Therapeutics, Inc. | $432.15M | Small cap | +6.92% | Nov 5, 2026 |
| XFOR | X4 Pharmaceuticals, Inc. | $412.45M | Small cap | −1.42% | Nov 5, 2026 |
| ENTA | Enanta Pharmaceuticals, Inc. | $412.12M | Small cap | +65.89% | Nov 16, 2026 |
| UPB | Upstream Bio, Inc. | $390.52M | Small cap | −57.31% | Nov 4, 2026 |
| IFRX | InflaRx N.V. | $356.63M | Small cap | +142.00% | Nov 9, 2026 |
| IKT | Inhibikase Therapeutics, Inc. | $347.44M | Small cap | +39.11% | Nov 13, 2026 |
| PRQR | ProQR Therapeutics N.V. | $331.63M | Small cap | +6.33% | Nov 5, 2026 |
| TRDA | Entrada Therapeutics, Inc. | $296.70M | Small cap | +23.24% | Nov 5, 2026 |
| FULC | Fulcrum Therapeutics, Inc. | $294.51M | Small cap | −41.78% | Oct 29, 2026 |
| TTRX | Turn Therapeutics Inc. | $292.44M | Small cap | +37.57% | Nov 12, 2026 |
| SION | Sionna Therapeutics, Inc. | $282.58M | Small cap | −75.45% | Nov 5, 2026 |
| ELDN | Eledon Pharmaceuticals, Inc. | $272.22M | Small cap | +29.84% | Nov 13, 2026 |
| IVVD | Invivyd, Inc. | $265.78M | Small cap | +3.52% | Nov 5, 2026 |
| SLGL | Sol-Gel Technologies Ltd. | $260.05M | Small cap | +261.87% | Nov 19, 2026 |
| AKBA | Akebia Therapeutics, Inc. | $251.20M | Small cap | −69.88% | Nov 9, 2026 |
| CRDL | Cardiol Therapeutics Inc. | $250.00M | Small cap | +91.07% | Nov 12, 2026 |
| PEPG | PepGen Inc. | $237.21M | Small cap | +159.68% | Nov 11, 2026 |
| SIGA | SIGA Technologies, Inc. | $220.58M | Small cap | −57.93% | Nov 5, 2026 |
| KROS | Keros Therapeutics, Inc. | $220.48M | Small cap | −28.35% | Nov 4, 2026 |
| ARMP | Armata Pharmaceuticals, Inc. | $202.64M | Small cap | +123.36% | Nov 11, 2026 |
| PLX | Protalix BioTherapeutics, Inc. | $199.82M | Small cap | +55.00% | Nov 12, 2026 |
| MSLE | Satellos Bioscience Inc. | $198.59M | Small cap | +77.27% | Nov 12, 2026 |
| MDWD | MediWound Ltd. | $163.96M | Small cap | −25.29% | Nov 19, 2026 |
| AARD | Aardvark Therapeutics, Inc. | $149.04M | Small cap | −24.25% | Nov 12, 2026 |
| MIST | Milestone Pharmaceuticals Inc. | $146.91M | Small cap | −33.33% | Nov 12, 2026 |
| INO | Inovio Pharmaceuticals, Inc. | $134.42M | Small cap | −47.15% | Nov 10, 2026 |
| CPIX | Cumberland Pharmaceuticals Inc. | $130.35M | Small cap | +163.82% | Nov 3, 2026 |
| RFL | Rafael Holdings, Inc. | $119.08M | Small cap | +52.67% | Oct 28, 2026 |
| PYPD | PolyPid Ltd. | $103.79M | Small cap | +49.42% | Nov 11, 2026 |
| PTHS | Pelthos Therapeutics Inc. | $102.53M | Small cap | +12.90% | Nov 12, 2026 |
Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.