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Rare disease stocks

We cover 51 companies grouped under the Rare disease theme. The median market value in the group is $2.60B. Across the group, the median move over the past trading day is −0.28%. 67% of the 49 with a 200-day average trade above it. Price change over the past year runs from −75.2% to +207.1% across the middle 80 percent of the group, with a median of +46.0%.

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Table

51 of 268 companies match these filters.Clear filters

TickerCompanyMarket cap (USD)Size1Y returnNext report
0HNC.LBioMarin Pharmaceutical Inc.$9.93BMid cap+15.03%Oct 26, 2026
PTGXProtagonist Therapeutics, Inc.$9.80BMid cap+146.62%Nov 5, 2026
IMVTImmunovant, Inc.$9.07BMid cap+189.13%Nov 9, 2026
CRNXCrinetics Pharmaceuticals, Inc.$9.00BMid cap+179.08%Nov 5, 2026
4151.TKyowa Kirin Co., Ltd.$8.51BMid cap+4.01%Nov 2, 2026
RYTMRhythm Pharmaceuticals, Inc.$7.78BMid cap+9.35%Nov 3, 2026
SRRKScholar Rock Holding Corporation$7.31BMid cap+74.18%Nov 12, 2026
ORKAOruka Therapeutics, Inc.$6.58BMid cap+555.07%Nov 11, 2026
LQDALiquidia Corporation$6.31BMid cap+154.86%Nov 3, 2026
TVTXTravere Therapeutics, Inc.$6.24BMid cap+284.86%Oct 29, 2026
DNTHDianthus Therapeutics, Inc.$6.13BMid cap+356.93%Nov 5, 2026
PTCTPTC Therapeutics, Inc. Common Stock$6.07BMid cap+46.02%Nov 5, 2026
KNSAKiniksa Pharmaceuticals International, plc$6.05BMid cap+133.47%Oct 27, 2026
MIRMMirum Pharmaceuticals, Inc.$5.98BMid cap+31.96%Nov 4, 2026
DYNDyne Therapeutics, Inc.$4.92BMid cap+93.26%Nov 5, 2026
EWTXEdgewise Therapeutics, Inc.$4.80BMid cap+207.13%Nov 5, 2026
MANEVeradermics, Incorporated$4.29BMid cap+172.32%Nov 12, 2026
AMLXAmylyx Pharmaceuticals, Inc.$4.13BMid cap+292.38%Nov 5, 2026
CAMX.STCamurus AB (publ)$3.79BMid cap−15.35%Nov 5, 2026
CLDXCelldex Therapeutics, Inc.$3.19BMid cap+79.51%Nov 9, 2026
IRONDisc Medicine, Inc.$3.17BMid cap+37.90%Nov 5, 2026
ARQTArcutis Biotherapeutics, Inc.$3.12BMid cap+60.64%Oct 27, 2026
VRDNViridian Therapeutics, Inc.$2.75BMid cap+30.71%Nov 5, 2026
VERAVera Therapeutics, Inc.$2.65BMid cap+67.21%Nov 5, 2026
RAREUltragenyx Pharmaceutical Inc.$2.61BMid cap−12.10%Nov 3, 2026
PHVSPharvaris N.V.$2.60BMid cap+55.59%Nov 12, 2026
TRVITrevi Therapeutics, Inc.$2.55BMid cap+124.00%Nov 12, 2026
NKTRNektar Therapeutics$2.52BMid cap+151.95%Nov 12, 2026
BCRXBioCryst Pharmaceuticals, Inc.$2.51BMid cap+15.38%Nov 2, 2026
COAGHemab Therapeutics Holdings, Inc.$2.30BMid cap+44.68%Nov 16, 2026
MLYSMineralys Therapeutics, Inc.$2.28BMid cap+70.22%Nov 10, 2026
PVLAPalvella Therapeutics, Inc.$2.22BMid cap+173.39%Nov 11, 2026
AUPHAurinia Pharmaceuticals Inc.$2.20BMid cap+36.58%Nov 9, 2026
ADMAADMA Biologics, Inc.$2.16BMid cap−44.17%Nov 4, 2026
ZBIOZenas BioPharma, Inc.$2.15BMid cap+97.73%Nov 12, 2026
STOKStoke Therapeutics, Inc.$2.14BMid cap+71.45%Nov 3, 2026
AGIOAgios Pharmaceuticals, Inc. Common Stock$2.03BMid cap−13.45%Oct 29, 2026
GOSSGossamer Bio, Inc.$85.01MMicro cap−92.93%Nov 4, 2026
SPROSpero Therapeutics, Inc.$71.05MMicro cap−38.38%Nov 12, 2026
SCYXSCYNEXIS, Inc.$56.41MMicro cap+579.04%Nov 4, 2026
ATYRaTyr Pharma, Inc.$54.05MMicro cap−89.34%Nov 5, 2026
MCRBSeres Therapeutics, Inc.$47.81MMicro cap−74.79%Nov 4, 2026
MREOMereo BioPharma Group plc$44.39MMicro cap−84.20%Nov 9, 2026
QNCXQuince Therapeutics, Inc.$31.84MMicro cap+100.71%Nov 12, 2026
RVX.TOResverlogix Corp.$24.81MMicro cap0.00%Nov 12, 2026
JSPRJasper Therapeutics, Inc.$23.96MMicro cap−75.24%Nov 10, 2026
TVRDTvardi Therapeutics, Inc.$23.74MMicro cap−94.18%Nov 12, 2026
INMInMed Pharmaceuticals Inc.$7.64MMicro cap−36.44%Sep 23, 2026
JAGXJaguar Health, Inc.$4.78MMicro cap−98.52%Nov 12, 2026
XRTXXORTX Therapeutics Inc.$4.03MMicro cap−43.99%Nov 12, 2026
APLI.TOAppili Therapeutics Inc.$1.44MMicro cap−25.00%Nov 12, 2026

Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.

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