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Rare disease stocks

We cover 79 companies grouped under the Rare disease theme. The median market value in the group is $81.15M. Across the group, the median move over the past trading day is +1.41%. 50% of the 76 with a 200-day average trade above it. Price change over the past year runs from −87.9% to +206.1% across the middle 80 percent of the group, with a median of +5.0%.

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Table

79 of 268 companies match these filters.Clear filters

TickerCompanyMarket cap (USD)Size1Y return
CRNXCrinetics Pharmaceuticals, Inc.$9.00BMid cap+182.02%
IMVTImmunovant, Inc.$8.95BMid cap+192.14%
RYTMRhythm Pharmaceuticals, Inc.$7.78BMid cap+14.26%
SRRKScholar Rock Holding Corporation$7.09BMid cap+74.77%
ORKAOruka Therapeutics, Inc.$6.74BMid cap+601.72%
LQDALiquidia Corporation$6.31BMid cap+168.53%
KNSAKiniksa Pharmaceuticals International, plc$6.17BMid cap+142.74%
PTCTPTC Therapeutics, Inc. Common Stock$6.13BMid cap+49.03%
DNTHDianthus Therapeutics, Inc.$6.13BMid cap+378.90%
TVTXTravere Therapeutics, Inc.$6.06BMid cap+288.91%
MIRMMirum Pharmaceuticals, Inc.$5.98BMid cap+36.58%
GRFSGrifols, S.A.$5.44BMid cap−17.62%
DYNDyne Therapeutics, Inc.$4.92BMid cap+102.62%
EWTXEdgewise Therapeutics, Inc.$4.80BMid cap+209.16%
AMLXAmylyx Pharmaceuticals, Inc.$4.17BMid cap+340.71%
MANEVeradermics, Incorporated$4.11BMid cap+171.13%
CPRXCatalyst Pharmaceuticals Inc$3.85BMid cap+52.72%
CLDXCelldex Therapeutics, Inc.$3.24BMid cap+87.96%
IRONDisc Medicine, Inc.$3.16BMid cap+38.71%
ARQTArcutis Biotherapeutics, Inc.$3.12BMid cap+58.44%
VRDNViridian Therapeutics, Inc.$2.74BMid cap+30.21%
PHVSPharvaris N.V.$2.62BMid cap+57.76%
RAREUltragenyx Pharmaceutical Inc.$2.61BMid cap−9.60%
TRVITrevi Therapeutics, Inc.$2.56BMid cap+146.57%
VERAVera Therapeutics, Inc.$2.54BMid cap+65.32%
NKTRNektar Therapeutics$2.52BMid cap+176.20%
BCRXBioCryst Pharmaceuticals, Inc.$2.51BMid cap+17.16%
MLYSMineralys Therapeutics, Inc.$2.32BMid cap+78.70%
COAGHemab Therapeutics Holdings, Inc.$2.32BMid cap+46.03%
AUPHAurinia Pharmaceuticals Inc.$2.23BMid cap+38.03%
ZBIOZenas BioPharma, Inc.$2.20BMid cap+103.93%
STOKStoke Therapeutics, Inc.$2.16BMid cap+77.32%
ADMAADMA Biologics, Inc.$2.14BMid cap−42.86%
PVLAPalvella Therapeutics, Inc.$2.14BMid cap+195.71%
GOSSGossamer Bio, Inc.$99.97MMicro cap−91.33%
FBIOFortress Biotech, Inc.$94.38MMicro cap+23.58%
PLYXPolaryx Therapeutics, Inc.$94.21MMicro cap−94.66%
RLYBRallybio Corporation$89.67MMicro cap+262.65%
TENXTenax Therapeutics, Inc.$86.82MMicro cap−60.81%
TELOTelomir Pharmaceuticals, Inc.$81.15MMicro cap−19.18%
FBIOPFortress Biotech, Inc.$71.45MMicro cap+141.55%
SPROSpero Therapeutics, Inc.$70.76MMicro cap−33.51%
RNTXRein Therapeutics Inc.$69.01MMicro cap−32.20%
IMAImageneBio, Inc.$63.80MMicro cap−60.78%
ATYRaTyr Pharma, Inc.$55.91MMicro cap−88.95%
SCYXSCYNEXIS, Inc.$51.64MMicro cap+514.20%
NSRXNasus Pharma Ltd.$48.01MMicro cap−48.69%
MCRBSeres Therapeutics, Inc.$46.81MMicro cap−74.00%
GRCEGrace Therapeutics, Inc.$46.28MMicro cap−32.31%
MREOMereo BioPharma Group plc$44.97MMicro cap−83.82%
EDSAEdesa Biotech, Inc.$42.90MMicro cap+83.88%
QNCXQuince Therapeutics, Inc.$34.05MMicro cap+95.76%
NNVCNanoViricides, Inc.$32.93MMicro cap−12.84%
BRNSBarinthus Biotherapeutics plc$26.96MMicro cap−44.77%
JSPRJasper Therapeutics, Inc.$23.96MMicro cap−75.67%
TVRDTvardi Therapeutics, Inc.$23.74MMicro cap−93.77%
RVX.TOResverlogix Corp.$23.62MMicro cap+5.00%
COCPCocrystal Pharma, Inc.$21.77MMicro cap−26.62%
VYNEVYNE Therapeutics Inc$19.07MMicro cap+8687.69%
KTTAPasithea Therapeutics Corp.$18.71MMicro cap−21.90%
CALCCalciMedica, Inc.$17.10MMicro cap−78.92%
CMMBChemomab Therapeutics Ltd.$16.85MMicro cap−33.91%
HINDVyome Holdings, Inc.$15.65MMicro cap−80.23%
QNRXQuoin Pharmaceuticals, Ltd.$10.18MMicro cap−31.02%
AZTRAzitra, Inc.$9.55MMicro cap−78.97%
IMRNImmuron Limited$9.20MMicro cap−36.84%
SNGXSoligenix, Inc.$8.81MMicro cap−87.06%
XCURExicure, Inc.$7.79MMicro cap−79.90%
INMInMed Pharmaceuticals Inc.$7.69MMicro cap−35.43%
PULMPulmatrix, Inc.$5.84MMicro cap−67.81%
JAGXJaguar Health, Inc.$4.78MMicro cap−98.52%
CVKDCadrenal Therapeutics, Inc.$4.74MMicro cap−87.58%
GLMDGalmed Pharmaceuticals Ltd.$4.48MMicro cap+205.34%
GRIGRI Bio, Inc.$4.28MMicro cap−95.14%
XRTXXORTX Therapeutics Inc.$4.11MMicro cap−44.74%
SXTP60 Degrees Pharmaceuticals, Inc.$3.97MMicro cap−78.10%
MTNBMatinas BioPharma Holdings, Inc.$2.90MMicro cap−90.82%
APLI.TOAppili Therapeutics Inc.$1.44MMicro cap−25.00%
VBIOValion Bio, Inc.$660.05KMicro cap−95.00%

Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.

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