Free tool

Rare disease stocks

We cover 23 companies grouped under the Rare disease theme. The median market value in the group is $3.12B. Across the group, the median move over the past trading day is +1.72%. 81% of the 21 with a 200-day average trade above it. Price change over the past year runs from +5.0% to +273.0% across the middle 80 percent of the group, with a median of +65.3%.

Other lists in this group

Table

23 of 268 companies match these filters.Clear filters

TickerCompanyMarket cap (USD)Size1Y returnNext report
0HNC.LBioMarin Pharmaceutical Inc.$9.93BMid cap+12.68%Oct 26, 2026
4151.TKyowa Kirin Co., Ltd.$8.51BMid cap+3.09%Nov 2, 2026
RYTMRhythm Pharmaceuticals, Inc.$7.78BMid cap+14.26%Nov 3, 2026
ORKAOruka Therapeutics, Inc.$6.74BMid cap+601.72%Nov 11, 2026
LQDALiquidia Corporation$6.31BMid cap+168.53%Nov 3, 2026
KNSAKiniksa Pharmaceuticals International, plc$6.17BMid cap+142.74%Oct 27, 2026
TVTXTravere Therapeutics, Inc.$6.06BMid cap+288.91%Oct 29, 2026
MIRMMirum Pharmaceuticals, Inc.$5.98BMid cap+36.58%Nov 4, 2026
EWTXEdgewise Therapeutics, Inc.$4.80BMid cap+209.16%Nov 5, 2026
AMLXAmylyx Pharmaceuticals, Inc.$4.17BMid cap+340.71%Nov 5, 2026
MANEVeradermics, Incorporated$4.11BMid cap+171.13%Nov 12, 2026
ARQTArcutis Biotherapeutics, Inc.$3.12BMid cap+58.44%Oct 27, 2026
VRDNViridian Therapeutics, Inc.$2.74BMid cap+30.21%Nov 5, 2026
PHVSPharvaris N.V.$2.62BMid cap+57.76%Nov 12, 2026
RAREUltragenyx Pharmaceutical Inc.$2.61BMid cap−9.60%Nov 3, 2026
VERAVera Therapeutics, Inc.$2.54BMid cap+65.32%Nov 5, 2026
NKTRNektar Therapeutics$2.52BMid cap+176.20%Nov 12, 2026
BCRXBioCryst Pharmaceuticals, Inc.$2.51BMid cap+17.16%Nov 2, 2026
MLYSMineralys Therapeutics, Inc.$2.32BMid cap+78.70%Nov 10, 2026
COAGHemab Therapeutics Holdings, Inc.$2.32BMid cap+46.03%Nov 16, 2026
ZBIOZenas BioPharma, Inc.$2.20BMid cap+103.93%Nov 12, 2026
STOKStoke Therapeutics, Inc.$2.16BMid cap+77.32%Nov 3, 2026
ADMAADMA Biologics, Inc.$2.14BMid cap−42.86%Nov 4, 2026

Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.

More ways to browse