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Rare disease stocks

We cover 33 companies grouped under the Rare disease theme. The median market value in the group is $3.17B. Across the group, the median move over the past trading day is −0.08%. 81% of the 31 with a 200-day average trade above it. Price change over the past year runs from −7.8% to +203.5% across the middle 80 percent of the group, with a median of +71.5%.

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Table

33 of 268 companies match these filters.Clear filters

TickerCompanyMarket cap (USD)Size1Y return
PTGXProtagonist Therapeutics, Inc.$9.80BMid cap+146.62%
IMVTImmunovant, Inc.$9.07BMid cap+189.13%
RYTMRhythm Pharmaceuticals, Inc.$7.78BMid cap+9.35%
SRRKScholar Rock Holding Corporation$7.31BMid cap+74.18%
ORKAOruka Therapeutics, Inc.$6.58BMid cap+555.07%
LQDALiquidia Corporation$6.31BMid cap+154.86%
TVTXTravere Therapeutics, Inc.$6.24BMid cap+284.86%
DNTHDianthus Therapeutics, Inc.$6.13BMid cap+356.93%
PTCTPTC Therapeutics, Inc. Common Stock$6.07BMid cap+46.02%
KNSAKiniksa Pharmaceuticals International, plc$6.05BMid cap+133.47%
MIRMMirum Pharmaceuticals, Inc.$5.98BMid cap+31.96%
GRFSGrifols, S.A.$5.38BMid cap−19.39%
DYNDyne Therapeutics, Inc.$4.92BMid cap+93.26%
EWTXEdgewise Therapeutics, Inc.$4.80BMid cap+207.13%
MANEVeradermics, Incorporated$4.29BMid cap+172.32%
CLDXCelldex Therapeutics, Inc.$3.19BMid cap+79.51%
IRONDisc Medicine, Inc.$3.17BMid cap+37.90%
ARQTArcutis Biotherapeutics, Inc.$3.12BMid cap+60.64%
VRDNViridian Therapeutics, Inc.$2.75BMid cap+30.71%
VERAVera Therapeutics, Inc.$2.65BMid cap+67.21%
RAREUltragenyx Pharmaceutical Inc.$2.61BMid cap−12.10%
PHVSPharvaris N.V.$2.60BMid cap+55.59%
TRVITrevi Therapeutics, Inc.$2.55BMid cap+124.00%
NKTRNektar Therapeutics$2.52BMid cap+151.95%
BCRXBioCryst Pharmaceuticals, Inc.$2.51BMid cap+15.38%
COAGHemab Therapeutics Holdings, Inc.$2.30BMid cap+44.68%
MLYSMineralys Therapeutics, Inc.$2.28BMid cap+70.22%
PVLAPalvella Therapeutics, Inc.$2.22BMid cap+173.39%
AUPHAurinia Pharmaceuticals Inc.$2.20BMid cap+36.58%
ADMAADMA Biologics, Inc.$2.16BMid cap−44.17%
ZBIOZenas BioPharma, Inc.$2.15BMid cap+97.73%
STOKStoke Therapeutics, Inc.$2.14BMid cap+71.45%
AGIOAgios Pharmaceuticals, Inc. Common Stock$2.03BMid cap−13.45%

Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.

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