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Rare disease stocks

We cover 83 companies grouped under the Rare disease theme. The median market value in the group is $381.21M. Across the group, the median move over the past trading day is +2.03%. 57% of the 80 with a 200-day average trade above it. Price change over the past year runs from −69.3% to +261.2% across the middle 80 percent of the group, with a median of +35.0%.

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Table

83 of 268 companies match these filters.Clear filters

TickerCompanyPrice1M returnYTD return1Y returnNext report
AGIOAgios Pharmaceuticals, Inc. Common Stock$33.90−8.30%+24.72%−9.02%Oct 29, 2026
SEPNSepterna, Inc.$41.30+23.32%+47.61%+245.32%Nov 9, 2026
ETONEton Pharmaceuticals, Inc.$63.05+49.02%+287.76%+268.93%Nov 12, 2026
ANIPANI Pharmaceuticals, Inc.$75.65−3.47%−3.54%−16.24%Nov 6, 2026
AVLNAvalyn Pharma Inc.$38.20+38.31%+29.54%+29.54%Nov 16, 2026
0L35.LSarepta Therapeutics, Inc.$18.94+3.95%−11.24%+4.63%Nov 4, 2026
MAZEMaze Therapeutics, Inc.$30.42+6.03%−23.51%+128.55%Nov 5, 2026
FBRXForte Biosciences, Inc.$76.97+0.61%+226.01%+580.25%Nov 9, 2026
TRAXFirst Tracks Biotherapeutics, Inc.$45.11+7.33%+137.42%+137.42%Nov 5, 2026
XERSXeris Biopharma Holdings, Inc.$8.74+6.46%+18.91%+12.48%Nov 5, 2026
TYRATyra Biosciences, Inc.$26.69−14.07%−0.37%+122.42%Nov 4, 2026
0LIF.LUltragenyx Pharmaceutical Inc.$26.69+3.33%+14.67%−11.63%Nov 3, 2026
OMEROmeros Corporation$19.28+70.02%+17.70%+343.22%Nov 12, 2026
JBIOJade Biosciences, Inc.$21.84+9.47%+54.24%+176.46%Nov 12, 2026
MLTXMoonLake Immunotherapeutics$15.56−21.73%+30.21%−71.52%Nov 5, 2026
0HB0.LAgios Pharmaceuticals, Inc.$33.99+2.11%+25.84%−14.25%Oct 29, 2026
SVRASavara Inc.$5.60+3.13%−0.71%+78.34%Nov 11, 2026
ANNXAnnexon, Inc.$5.15+0.39%+9.81%+139.53%Nov 9, 2026
DBVTDBV Technologies S.A.$14.97+7.70%−21.42%+52.91%Oct 28, 2026
DBV.PADBV Technologies S.A.2.44 EUR+2.78%−25.33%+54.11%Oct 28, 2026
SLNSilence Therapeutics plc$13.67+13.26%+122.28%+170.16%Nov 5, 2026
GNFT.PAGenfit S.A.13.90 EUR+5.30%+164.76%+293.99%Sep 29, 2026
STTKShattuck Labs, Inc.$8.06+14.49%+117.25%+710.87%Nov 12, 2026
TECXTectonic Therapeutic, Inc.$37.71+23.20%+80.34%+53.48%Nov 5, 2026
ZVRAZevra Therapeutics, Inc.$12.04+24.00%+44.36%+28.63%Nov 4, 2026
GYREGyre Therapeutics, Inc.$6.68+8.97%−1.91%−18.54%Nov 5, 2026
CRMDCorMedix Inc.$8.56+12.63%−29.61%−37.65%Nov 16, 2026
ZURAZura Bio Limited$6.32+17.47%+13.87%+208.29%Nov 12, 2026
AQSTAquestive Therapeutics, Inc.$5.08+36.19%−21.24%+31.61%Nov 4, 2026
0KBU.LOmeros Corporation$19.34−0.10%+16.56%+341.05%Nov 12, 2026
SPRYARS Pharmaceuticals, Inc.$5.72−0.69%−50.22%−57.66%Nov 10, 2026
KMDAKamada Ltd. Ordinary Shares$8.63+23.46%+26.48%+26.12%Nov 9, 2026
EPRXEupraxia Pharmaceuticals Inc.$7.42+20.26%−1.98%+41.87%Nov 3, 2026
EPRX.TOEupraxia Pharmaceuticals Inc.10.20 CAD+16.70%−2.49%+41.67%Nov 3, 2026
RZLTRezolute, Inc.$5.01+1.42%+131.41%−28.43%Sep 16, 2026
AVIRAtea Pharmaceuticals, Inc.$5.43+12.66%+56.03%+48.36%Nov 11, 2026
LRMRLarimar Therapeutics, Inc.$4.16+8.62%+19.88%+11.83%Nov 5, 2026
XFORX4 Pharmaceuticals, Inc.$4.16+5.58%+6.94%+4.79%Nov 5, 2026
ENTAEnanta Pharmaceuticals, Inc.$14.08+10.60%−2.36%+62.59%Nov 16, 2026
4552.TJCR Pharmaceuticals Co., Ltd.545.00 JPY+5.21%−19.79%−7.40%Oct 29, 2026
UPBUpstream Bio, Inc.$7.18+12.19%−73.48%−57.08%Nov 4, 2026
CUV.AXClinuvel Pharmaceuticals Limited10.54 AUD+7.44%−17.07%−21.84%Aug 27, 2026
IKTInhibikase Therapeutics, Inc.$2.50+6.38%+28.21%+42.05%Nov 13, 2026
PRQRProQR Therapeutics N.V.$2.38+37.57%+19.60%+5.78%Nov 5, 2026
TRDAEntrada Therapeutics, Inc.$7.62+25.33%−24.18%+35.35%Nov 5, 2026
TTRXTurn Therapeutics Inc.$9.73+25.06%+107.46%+39.00%Nov 12, 2026
FULCFulcrum Therapeutics, Inc.$3.86+3.49%−64.65%−39.78%Oct 29, 2026
SIONSionna Therapeutics, Inc.$6.25−86.23%−84.06%−74.02%Nov 5, 2026
ELDNEledon Pharmaceuticals, Inc.$3.47−2.80%+114.20%+35.02%Nov 13, 2026
IVVDInvivyd, Inc.$0.94+53.89%−62.45%+67.62%Nov 5, 2026
SLGLSol-Gel Technologies Ltd.$81.72+2.37%+93.88%+289.14%Nov 19, 2026
XUP.DEGenfit S.A.14.08 EUR−1.81%+164.41%+166.82%Sep 29, 2026
CRDLCardiol Therapeutics Inc.$2.00+73.16%+101.21%+75.44%Nov 12, 2026
CRDL.TOCardiol Therapeutics Inc.2.76 CAD+68.29%+102.94%+72.50%Nov 12, 2026
SIGASIGA Technologies, Inc.$3.04−1.94%−45.19%−60.50%Nov 5, 2026
ARMPArmata Pharmaceuticals, Inc.$5.56+7.96%−15.24%+113.85%Nov 11, 2026
MSLESatellos Bioscience Inc.$9.40−0.58%+51.52%+82.17%Nov 12, 2026
MSCL.TOSatellos Bioscience Inc.13.00 CAD−2.26%+54.76%+80.56%Nov 12, 2026
PLXProtalix BioTherapeutics, Inc.$2.41+0.42%+38.51%+50.62%Nov 12, 2026
0AB6.LHyloris Pharmaceuticals SA4.46 EUR−0.66%−37.71%−32.01%Sep 24, 2026
AARDAardvark Therapeutics, Inc.$7.25+8.37%−45.03%−19.80%Nov 12, 2026
MISTMilestone Pharmaceuticals Inc.$1.16+2.65%−43.41%−31.36%Nov 12, 2026
CPIXCumberland Pharmaceuticals Inc.$8.70+59.59%+118.59%+166.87%Nov 3, 2026
INOInovio Pharmaceuticals, Inc.$1.29+32.99%−23.67%−33.85%Nov 10, 2026
0H8T.LAclaris Therapeutics, Inc.$6.58+6.50%+120.68%+265.21%Nov 5, 2026
MDP.TOMedexus Pharmaceuticals Inc.5.15 CAD+3.83%+66.67%+80.70%Nov 11, 2026
RFLRafael Holdings, Inc.$2.24−1.75%+77.78%+52.38%Oct 28, 2026
PTHSPelthos Therapeutics Inc.$27.20−1.41%−7.64%+20.41%Nov 12, 2026
PYPDPolyPid Ltd.$5.10+28.14%+17.24%+47.83%Nov 11, 2026
GOSSGossamer Bio, Inc.$0.20+2.76%−92.90%−91.33%Nov 4, 2026
SPROSpero Therapeutics, Inc.$1.23+4.24%−47.66%−33.51%Nov 12, 2026
ATYRaTyr Pharma, Inc.$0.57+16.33%−24.90%−88.95%Nov 5, 2026
SCYXSCYNEXIS, Inc.$5.19+45.38%+712.21%+514.20%Nov 4, 2026
MCRBSeres Therapeutics, Inc.$5.00+3.09%−67.00%−74.00%Nov 4, 2026
MREOMereo BioPharma Group plc$0.28−6.75%−44.78%−83.82%Nov 9, 2026
QNCXQuince Therapeutics, Inc.$30.93+73.28%+3.10%+95.76%Nov 12, 2026
JSPRJasper Therapeutics, Inc.$0.72+3.78%−60.86%−75.67%Nov 10, 2026
TVRDTvardi Therapeutics, Inc.$1.82−28.35%−55.39%−93.77%Nov 12, 2026
RVX.TOResverlogix Corp.0.11 CAD−4.55%+5.00%+5.00%Nov 12, 2026
INMInMed Pharmaceuticals Inc.$1.44−12.20%+28.57%−35.43%Sep 23, 2026
JAGXJaguar Health, Inc.$0.92−7.51%−97.35%−98.52%Nov 12, 2026
XRTXXORTX Therapeutics Inc.$2.26+11.88%−20.70%−44.74%Nov 12, 2026
APLI.TOAppili Therapeutics Inc.0.02 CAD+50.00%−40.00%−25.00%Nov 12, 2026

Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.

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