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Rare disease stocks
We cover 48 companies grouped under the Rare disease theme. The median market value in the group is $246.69M. Across the group, the median move over the past trading day is +0.43%. 40% of the 42 with a 200-day average trade above it. Price change over the past year runs from −51.6% to +68.7% across the middle 80 percent of the group, with a median of −9.0%.
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Table
48 of 268 companies match these filters.Clear filters
| Ticker | Company | Price | 1M return | YTD return | 1Y return |
|---|---|---|---|---|---|
| VX1.DE | Vertex Pharmaceuticals Incorporated | 475.00 EUR | +10.21% | +23.55% | +41.64% |
| DUL.DE | Alnylam Pharmaceuticals, Inc. | 204.00 EUR | −19.59% | −40.19% | −10.21% |
| 0JAV.L | Insmed Incorporated | $125.00 | +0.43% | −28.28% | −7.52% |
| REC.MI | Recordati Industria Chimica e Farmaceutica S.p.A. | 52.70 EUR | +2.53% | +10.68% | +1.80% |
| 0JDI.L | Ionis Pharmaceuticals, Inc. | $63.37 | +3.44% | −19.72% | +47.26% |
| ABVX.PA | ABIVAX Société Anonyme | 102.30 EUR | −5.63% | −11.04% | +48.91% |
| 0HI3.L | Arrowhead Pharmaceuticals, Inc. | $89.35 | +3.26% | +32.80% | +294.59% |
| CAMX.ST | Camurus AB (publ) | 615.00 SEK | −1.68% | +0.49% | −15.35% |
| 0RD1.L | Camurus AB (publ) | 609.98 SEK | −0.21% | −0.53% | −15.10% |
| 0L35.L | Sarepta Therapeutics, Inc. | $18.51 | +1.60% | −13.25% | −0.06% |
| 0LIF.L | Ultragenyx Pharmaceutical Inc. | $26.19 | +1.39% | +12.52% | −13.39% |
| 0HB0.L | Agios Pharmaceuticals, Inc. | $34.05 | +0.18% | +26.06% | −13.00% |
| DBV.PA | DBV Technologies S.A. | 2.53 EUR | +5.42% | −22.51% | +60.13% |
| GNFT.PA | Genfit S.A. | 14.30 EUR | +5.30% | +172.38% | +310.45% |
| AYJ.DE | Valneva SE | 2.98 EUR | +35.29% | −23.93% | −21.89% |
| 0QN1.L | Santhera Pharmaceuticals Holding AG | 15.66 CHF | −1.88% | +29.00% | +11.86% |
| 0T6G.L | Q32 Bio Inc. | $16.34 | +7.94% | — | — |
| 0AB6.L | Hyloris Pharmaceuticals SA | 4.38 EUR | −1.79% | −38.83% | −33.23% |
| CRNO-B.ST | Cereno Scientific AB (publ) | 4.71 SEK | +0.13% | −32.04% | −53.59% |
| 0H8T.L | Aclaris Therapeutics, Inc. | $6.14 | −6.69% | +105.92% | +237.38% |
| ABNX.PA | ABIONYX Pharma SA | 1.97 EUR | +5.79% | −49.58% | −31.34% |
| 0RAG.L | ABIONYX Pharma SA | 2.01 EUR | +3.40% | −48.40% | −29.10% |
| STX.L | Shield Therapeutics plc | 4.85 GBP | −15.65% | −50.76% | −37.42% |
| ALTHX.PA | THX Pharma Société Anonyme | 4.18 EUR | +5.16% | +83.92% | +73.96% |
| IMM.L | ImmuPharma plc | 3.41 GBP | −24.22% | −45.00% | +89.66% |
| ALDVI.PA | Advicenne S.A. | 1.75 EUR | +4.79% | −6.02% | +39.11% |
| 0RQJ.L | Saniona AB (publ) | 11.80 SEK | +0.47% | −44.08% | −12.20% |
| ALBPS.PA | Biophytis S.A. | 0.08 EUR | +422.88% | +28.41% | −50.31% |
| ANNX.ST | Annexin Pharmaceuticals AB (publ) | 13.60 SEK | +7.09% | −31.66% | −46.03% |
| PHR.WA | Pharmena S.A. | 3.14 PLN | +1.62% | +18.49% | −8.72% |
| BIOSGN.ST | Biosergen AB (publ) | 2.48 SEK | +262.31% | −93.80% | −94.62% |
| APTA.ST | Aptahem AB (publ) | 0.56 SEK | −15.96% | −51.69% | −67.65% |
| ALNEV.PA | Neovacs S.A. | 0.55 EUR | −31.22% | +6150.00% | −11.29% |
| 0A43.L | Inovio Pharmaceuticals, Inc. | $1.32 | +4.35% | −20.55% | −44.09% |
| 0A4D.L | Equillium, Inc. | $2.41 | +10.15% | +63.95% | +37.32% |
| 0A6I.L | Soligenix, Inc. | $0.39 | −4.04% | −71.78% | −87.16% |
| 0A9G.L | Mereo BioPharma Group plc | $0.28 | −2.36% | −42.56% | −84.25% |
| 0QNS.L | Curatis Holding AG | 19.05 CHF | 0.00% | −15.71% | −15.71% |
| 0UNL.L | Nektar Therapeutics | $74.20 | +6.73% | +14.04% | +14.04% |
| 1AE.DE | argenx SE | 898.60 EUR | +15.89% | +24.05% | +38.37% |
| 2X1.DE | ABIVAX Société Anonyme | 100.50 EUR | −6.77% | −12.30% | +33.82% |
| BIOV.SW | BioVersys AG | 25.20 CHF | −6.67% | +6.33% | −9.03% |
| BPBS.PA | BIOPHYTIS BSA | 0.00 EUR | 0.00% | 0.00% | 0.00% |
| CESSA.CO | Cessatech A/S | 9.42 DKK | +9.53% | −48.38% | −48.38% |
| CURN.SW | Curatis Holding AG | 19.00 CHF | −11.21% | +45.59% | +65.22% |
| DBV.DE | DBV Technologies S.A. | 2.46 EUR | +12.83% | −25.17% | +64.35% |
| PHGN.DE | Pharming Group N.V. | 0.98 EUR | −10.95% | −32.74% | −21.41% |
| SANN.SW | Santhera Pharmaceuticals Holding AG | 15.70 CHF | +9.79% | +29.32% | +13.44% |
Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.