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Rare disease stocks
We cover 99 companies grouped under the Rare disease theme. The median market value in the group is $46.28M. Across the group, the median move over the past trading day is +0.69%. 39% of the 95 with a 200-day average trade above it. Price change over the past year runs from −87.2% to +109.0% across the middle 80 percent of the group, with a median of −22.4%.
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Table
99 of 268 companies match these filters.Clear filters
| Ticker | Company | Market cap (USD) | Size | 1Y return |
|---|---|---|---|---|
| VX1.DE | Vertex Pharmaceuticals Incorporated | $140.77B | Large cap | +40.14% |
| VRTX34.SA | Vertex Pharmaceuticals Incorporated | $140.14B | Large cap | −83.17% |
| VRTX | Vertex Pharmaceuticals Incorporated | $140.04B | Large cap | +42.14% |
| 0QZU.L | Vertex Pharmaceuticals Incorporated | $112.52B | Large cap | +42.39% |
| ARGX | argenx SE | $63.78B | Large cap | +50.52% |
| A1RG34.SA | argenx SE | $63.17B | Large cap | +44.49% |
| 0HD2.L | Alnylam Pharmaceuticals, Inc. | $35.05B | Large cap | −46.85% |
| ALNY | Alnylam Pharmaceuticals, Inc. | $32.12B | Large cap | −45.88% |
| DUL.DE | Alnylam Pharmaceuticals, Inc. | $31.87B | Large cap | −11.75% |
| A1LN34.SA | Alnylam Pharmaceuticals, Inc. | $31.78B | Large cap | −49.89% |
| INSM | Insmed Incorporated | $27.07B | Large cap | −3.45% |
| ROIV | Roivant Sciences Ltd. | $26.26B | Large cap | +213.32% |
| JAZZ | Jazz Pharmaceuticals plc | $16.89B | Large cap | +108.87% |
| ASND | Ascendis Pharma A/S | $16.59B | Large cap | +32.89% |
| BBIO | BridgeBio Pharma, Inc. | $15.85B | Large cap | +70.01% |
| CORT | Corcept Therapeutics Incorporated | $13.36B | Large cap | +79.56% |
| 0JAV.L | Insmed Incorporated | $12.89B | Large cap | −6.25% |
| BMRN | BioMarin Pharmaceutical Inc. | $12.80B | Large cap | +13.03% |
| REC.MI | Recordati Industria Chimica e Farmaceutica S.p.A. | $12.60B | Large cap | +2.09% |
| B1MR34.SA | BioMarin Pharmaceutical Inc. | $12.54B | Large cap | +6.36% |
| ARWR | Arrowhead Pharmaceuticals, Inc. | $12.52B | Large cap | +329.16% |
| CYTK | Cytokinetics, Incorporated | $10.77B | Large cap | +109.29% |
| IONS | Ionis Pharmaceuticals, Inc. | $10.56B | Large cap | +52.01% |
| KYMR | Kymera Therapeutics, Inc. | $10.53B | Large cap | +202.82% |
| ABVX.PA | ABIVAX Société Anonyme | $10.42B | Large cap | +42.59% |
| 0JDI.L | Ionis Pharmaceuticals, Inc. | $10.40B | Large cap | +49.07% |
| PTGX | Protagonist Therapeutics, Inc. | $10.01B | Large cap | +164.75% |
| GOSS | Gossamer Bio, Inc. | $99.97M | Micro cap | −91.33% |
| ILA.AX | Island Pharmaceuticals Limited | $99.59M | Micro cap | +104.35% |
| ABNX.PA | ABIONYX Pharma SA | $97.56M | Micro cap | −16.20% |
| PAR.AX | Paradigm Biopharmaceuticals Limited | $96.60M | Micro cap | −22.41% |
| 0RAG.L | ABIONYX Pharma SA | $95.77M | Micro cap | −18.26% |
| FBIO | Fortress Biotech, Inc. | $94.38M | Micro cap | +23.58% |
| PLYX | Polaryx Therapeutics, Inc. | $94.21M | Micro cap | −94.66% |
| RLYB | Rallybio Corporation | $89.67M | Micro cap | +262.65% |
| TENX | Tenax Therapeutics, Inc. | $86.82M | Micro cap | −60.81% |
| TELO | Telomir Pharmaceuticals, Inc. | $81.15M | Micro cap | −19.18% |
| RCE.AX | Recce Pharmaceuticals Ltd | $81.01M | Micro cap | −12.79% |
| FBIOP | Fortress Biotech, Inc. | $71.45M | Micro cap | +141.55% |
| STX.L | Shield Therapeutics plc | $70.81M | Micro cap | −41.98% |
| SPRO | Spero Therapeutics, Inc. | $70.76M | Micro cap | −33.51% |
| ALTHX.PA | THX Pharma Société Anonyme | $70.40M | Micro cap | +89.35% |
| RNTX | Rein Therapeutics Inc. | $69.01M | Micro cap | −32.20% |
| IMA | ImageneBio, Inc. | $63.80M | Micro cap | −60.78% |
| 0IIM.L | Esperion Therapeutics, Inc. | $61.56M | Micro cap | +46.64% |
| ATYR | aTyr Pharma, Inc. | $55.91M | Micro cap | −88.95% |
| SCYX | SCYNEXIS, Inc. | $51.64M | Micro cap | +514.20% |
| NSRX | Nasus Pharma Ltd. | $48.01M | Micro cap | −48.69% |
| MCRB | Seres Therapeutics, Inc. | $46.81M | Micro cap | −74.00% |
| GRCE | Grace Therapeutics, Inc. | $46.28M | Micro cap | −32.31% |
| MREO | Mereo BioPharma Group plc | $44.97M | Micro cap | −83.82% |
| EDSA | Edesa Biotech, Inc. | $42.90M | Micro cap | +83.88% |
| BOT.AX | Botanix Pharmaceuticals Limited | $39.22M | Micro cap | −87.10% |
| QNCX | Quince Therapeutics, Inc. | $34.05M | Micro cap | +95.76% |
| NNVC | NanoViricides, Inc. | $32.93M | Micro cap | −12.84% |
| 520A.T | J-PHARMACEUTICALS CO LTD | $31.08M | Micro cap | −60.71% |
| ALDVI.PA | Advicenne S.A. | $29.99M | Micro cap | +41.44% |
| 4591.T | Ribomic Inc. | $29.85M | Micro cap | −22.94% |
| IMM.L | ImmuPharma plc | $29.03M | Micro cap | +83.56% |
| 0RQJ.L | Saniona AB (publ) | $27.98M | Micro cap | −13.86% |
| BRNS | Barinthus Biotherapeutics plc | $26.96M | Micro cap | −44.77% |
| JSPR | Jasper Therapeutics, Inc. | $23.96M | Micro cap | −75.67% |
| TVRD | Tvardi Therapeutics, Inc. | $23.74M | Micro cap | −93.77% |
| RVX.TO | Resverlogix Corp. | $23.62M | Micro cap | +5.00% |
| 4884.T | Kringle Pharma, Inc. | $22.99M | Micro cap | −7.41% |
| COCP | Cocrystal Pharma, Inc. | $21.77M | Micro cap | −26.62% |
| VYNE | VYNE Therapeutics Inc | $19.07M | Micro cap | +8687.69% |
| KTTA | Pasithea Therapeutics Corp. | $18.71M | Micro cap | −21.90% |
| CALC | CalciMedica, Inc. | $17.10M | Micro cap | −78.92% |
| CMMB | Chemomab Therapeutics Ltd. | $16.85M | Micro cap | −33.91% |
| 4881.T | FunPep Company Limited | $15.92M | Micro cap | −56.14% |
| HIND | Vyome Holdings, Inc. | $15.65M | Micro cap | −80.23% |
| ALBPS.PA | Biophytis S.A. | $12.86M | Micro cap | −53.47% |
| ANNX.ST | Annexin Pharmaceuticals AB (publ) | $10.31M | Micro cap | −49.23% |
| QNRX | Quoin Pharmaceuticals, Ltd. | $10.18M | Micro cap | −31.02% |
| AZTR | Azitra, Inc. | $9.55M | Micro cap | −78.97% |
| PHR.WA | Pharmena S.A. | $9.49M | Micro cap | −7.51% |
| IMRN | Immuron Limited | $9.20M | Micro cap | −36.84% |
| SNGX | Soligenix, Inc. | $8.81M | Micro cap | −87.06% |
| IMC.AX | Immuron Limited | $8.33M | Micro cap | −46.38% |
| XCUR | Exicure, Inc. | $7.79M | Micro cap | −79.90% |
| INM | InMed Pharmaceuticals Inc. | $7.69M | Micro cap | −35.43% |
| VBS.AX | Vectus Biosystems Limited | $6.65M | Micro cap | +87.50% |
| PULM | Pulmatrix, Inc. | $5.84M | Micro cap | −67.81% |
| BIOSGN.ST | Biosergen AB (publ) | $5.62M | Micro cap | −95.33% |
| JAGX | Jaguar Health, Inc. | $4.78M | Micro cap | −98.52% |
| CVKD | Cadrenal Therapeutics, Inc. | $4.74M | Micro cap | −87.58% |
| GLMD | Galmed Pharmaceuticals Ltd. | $4.48M | Micro cap | +205.34% |
| GRI | GRI Bio, Inc. | $4.28M | Micro cap | −95.14% |
| XRTX | XORTX Therapeutics Inc. | $4.11M | Micro cap | −44.74% |
| BIT.AX | Biotron Limited | $3.99M | Micro cap | −33.33% |
| SXTP | 60 Degrees Pharmaceuticals, Inc. | $3.97M | Micro cap | −78.10% |
| MTNB | Matinas BioPharma Holdings, Inc. | $2.90M | Micro cap | −90.82% |
| ANR.AX | Anatara Lifesciences Ltd | $2.04M | Micro cap | +12.50% |
| APTA.ST | Aptahem AB (publ) | $1.53M | Micro cap | −72.50% |
| APLI.TO | Appili Therapeutics Inc. | $1.44M | Micro cap | −25.00% |
| VBIO | Valion Bio, Inc. | $660.05K | Micro cap | −95.00% |
| 0R55.L | BioSenic S.A. | $26.40K | Micro cap | −23.08% |
| ALNEV.PA | Neovacs S.A. | $29.00 | Micro cap | −11.54% |
Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.