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Rare disease stocks
We cover 29 companies grouped under the Rare disease theme. The median market value in the group is $10.01B. Across the group, the median move over the past trading day is +0.70%. 43% of the 28 with a 200-day average trade above it. Price change over the past year runs from −89.4% to +120.4% across the middle 80 percent of the group, with a median of −6.3%.
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SaaSAI applicationsCybersecuritySemiconductor designSemiconductor equipmentFintech softwarePayment processingEcommerce marketplacesStreaming mediaGaming softwareOncologyRare diseaseMedical devicesCell therapyDiagnosticsRegional banksAsset managementGold miningCryptocurrency and digital assetsSpecialty chemicalsAll stocks
Table
29 of 268 companies match these filters.Clear filters
| Ticker | Company | Market cap (USD) | Size | 1Y return | Next report |
|---|---|---|---|---|---|
| VX1.DE | Vertex Pharmaceuticals Incorporated | $140.77B | Large cap | +40.14% | Nov 2, 2026 |
| VRTX | Vertex Pharmaceuticals Incorporated | $140.04B | Large cap | +42.14% | Nov 2, 2026 |
| 0QZU.L | Vertex Pharmaceuticals Incorporated | $112.52B | Large cap | +42.39% | Nov 2, 2026 |
| ARGX | argenx SE | $63.78B | Large cap | +50.52% | Oct 22, 2026 |
| 0HD2.L | Alnylam Pharmaceuticals, Inc. | $35.05B | Large cap | −46.85% | Oct 29, 2026 |
| ALNY | Alnylam Pharmaceuticals, Inc. | $32.12B | Large cap | −45.88% | Oct 29, 2026 |
| DUL.DE | Alnylam Pharmaceuticals, Inc. | $31.87B | Large cap | −11.75% | Oct 29, 2026 |
| INSM | Insmed Incorporated | $27.07B | Large cap | −3.45% | Oct 29, 2026 |
| BBIO | BridgeBio Pharma, Inc. | $15.85B | Large cap | +70.01% | Oct 28, 2026 |
| 0JAV.L | Insmed Incorporated | $12.89B | Large cap | −6.25% | Oct 29, 2026 |
| BMRN | BioMarin Pharmaceutical Inc. | $12.80B | Large cap | +13.03% | Oct 26, 2026 |
| CYTK | Cytokinetics, Incorporated | $10.77B | Large cap | +109.29% | Nov 5, 2026 |
| KYMR | Kymera Therapeutics, Inc. | $10.53B | Large cap | +202.82% | Nov 3, 2026 |
| ABVX.PA | ABIVAX Société Anonyme | $10.42B | Large cap | +42.59% | Sep 21, 2026 |
| PTGX | Protagonist Therapeutics, Inc. | $10.01B | Large cap | +164.75% | Nov 5, 2026 |
| GOSS | Gossamer Bio, Inc. | $99.97M | Micro cap | −91.33% | Nov 4, 2026 |
| SPRO | Spero Therapeutics, Inc. | $70.76M | Micro cap | −33.51% | Nov 12, 2026 |
| ATYR | aTyr Pharma, Inc. | $55.91M | Micro cap | −88.95% | Nov 5, 2026 |
| SCYX | SCYNEXIS, Inc. | $51.64M | Micro cap | +514.20% | Nov 4, 2026 |
| MCRB | Seres Therapeutics, Inc. | $46.81M | Micro cap | −74.00% | Nov 4, 2026 |
| MREO | Mereo BioPharma Group plc | $44.97M | Micro cap | −83.82% | Nov 9, 2026 |
| QNCX | Quince Therapeutics, Inc. | $34.05M | Micro cap | +95.76% | Nov 12, 2026 |
| JSPR | Jasper Therapeutics, Inc. | $23.96M | Micro cap | −75.67% | Nov 10, 2026 |
| TVRD | Tvardi Therapeutics, Inc. | $23.74M | Micro cap | −93.77% | Nov 12, 2026 |
| RVX.TO | Resverlogix Corp. | $23.62M | Micro cap | +5.00% | Nov 12, 2026 |
| INM | InMed Pharmaceuticals Inc. | $7.69M | Micro cap | −35.43% | Sep 23, 2026 |
| JAGX | Jaguar Health, Inc. | $4.78M | Micro cap | −98.52% | Nov 12, 2026 |
| XRTX | XORTX Therapeutics Inc. | $4.11M | Micro cap | −44.74% | Nov 12, 2026 |
| APLI.TO | Appili Therapeutics Inc. | $1.44M | Micro cap | −25.00% | Nov 12, 2026 |
Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.