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Rare disease stocks
We cover 65 companies grouped under the Rare disease theme. The median market value in the group is $264.31M. Across the group, the median move over the past trading day is +0.18%. 49% of the 57 with a 200-day average trade above it. Price change over the past year runs from −52.6% to +85.0% across the middle 80 percent of the group, with a median of −3.8%. Across the group, 1 company currently carries a tier A volume signal.
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Table
65 of 268 companies match these filters.Clear filters
| Ticker | Company | Price | 1M return | YTD return | 1Y return |
|---|---|---|---|---|---|
| VX1.DE | Vertex Pharmaceuticals Incorporated | 475.00 EUR | +10.21% | +23.55% | +41.64% |
| 0QZU.L | Vertex Pharmaceuticals Incorporated | $549.02 | +0.13% | +22.11% | +40.77% |
| 0HD2.L | Alnylam Pharmaceuticals, Inc. | $241.82 | +0.67% | −39.23% | −46.60% |
| DUL.DE | Alnylam Pharmaceuticals, Inc. | 204.00 EUR | −19.59% | −40.19% | −10.21% |
| 0JAV.L | Insmed Incorporated | $125.00 | +0.43% | −28.28% | −7.52% |
| REC.MI | Recordati Industria Chimica e Farmaceutica S.p.A. | 52.70 EUR | +2.53% | +10.68% | +1.80% |
| 0JDI.L | Ionis Pharmaceuticals, Inc. | $63.37 | +3.44% | −19.72% | +47.26% |
| ABVX.PA | ABIVAX Société Anonyme | 102.30 EUR | −5.63% | −11.04% | +48.91% |
| 0HNC.L | BioMarin Pharmaceutical Inc. | $66.19 | +0.05% | +11.54% | +15.03% |
| 0HI3.L | Arrowhead Pharmaceuticals, Inc. | $89.35 | +3.26% | +32.80% | +294.59% |
| CAMX.ST | Camurus AB (publ) | 615.00 SEK | −1.68% | +0.49% | −15.35% |
| 0RD1.L | Camurus AB (publ) | 609.98 SEK | −0.21% | −0.53% | −15.10% |
| 0L35.L | Sarepta Therapeutics, Inc. | $18.51 | +1.60% | −13.25% | −0.06% |
| 0LIF.L | Ultragenyx Pharmaceutical Inc. | $26.19 | +1.39% | +12.52% | −13.39% |
| 0HB0.L | Agios Pharmaceuticals, Inc. | $34.05 | +0.18% | +26.06% | −13.00% |
| DBV.PA | DBV Technologies S.A. | 2.53 EUR | +5.42% | −22.51% | +60.13% |
| GNFT.PA | Genfit S.A. | 14.30 EUR | +5.30% | +172.38% | +310.45% |
| 0QNA.L | Basilea Pharmaceutica AG | 65.80 CHF | +2.73% | +20.16% | +41.96% |
| AYJ.DE | Valneva SE | 2.98 EUR | +35.29% | −23.93% | −21.89% |
| 0KBU.L | Omeros Corporation | $18.44 | −4.75% | +11.14% | +332.86% |
| 0OB3.L | Valneva SE | 2.87 EUR | +0.75% | −23.95% | −25.05% |
| XUP.DE | Genfit S.A. | 14.08 EUR | −1.81% | +164.41% | +166.82% |
| 0QN1.L | Santhera Pharmaceuticals Holding AG | 15.66 CHF | −1.88% | +29.00% | +11.86% |
| 0T6G.L | Q32 Bio Inc. | $16.34 | +7.94% | — | — |
| 0AB6.L | Hyloris Pharmaceuticals SA | 4.38 EUR | −1.79% | −38.83% | −33.23% |
| CRNO-B.ST | Cereno Scientific AB (publ) | 4.71 SEK | +0.13% | −32.04% | −53.59% |
| 0H8T.L | Aclaris Therapeutics, Inc. | $6.14 | −6.69% | +105.92% | +237.38% |
| ABNX.PA | ABIONYX Pharma SA | 1.97 EUR | +5.79% | −49.58% | −31.34% |
| 0RAG.L | ABIONYX Pharma SA | 2.01 EUR | +3.40% | −48.40% | −29.10% |
| STX.L | Shield Therapeutics plc | 4.85 GBP | −15.65% | −50.76% | −37.42% |
| ALTHX.PA | THX Pharma Société Anonyme | 4.18 EUR | +5.16% | +83.92% | +73.96% |
| 0IIM.L | Esperion Therapeutics, Inc. | $3.19 | +0.14% | −14.28% | +44.65% |
| IMM.L | ImmuPharma plc | 3.41 GBP | −24.22% | −45.00% | +89.66% |
| ALDVI.PA | Advicenne S.A. | 1.75 EUR | +4.79% | −6.02% | +39.11% |
| 0RQJ.L | Saniona AB (publ) | 11.80 SEK | +0.47% | −44.08% | −12.20% |
| ALBPS.PA | Biophytis S.A. | 0.08 EUR | +422.88% | +28.41% | −50.31% |
| ANNX.ST | Annexin Pharmaceuticals AB (publ) | 13.60 SEK | +7.09% | −31.66% | −46.03% |
| PHR.WA | Pharmena S.A. | 3.14 PLN | +1.62% | +18.49% | −8.72% |
| BIOSGN.ST | Biosergen AB (publ) | 2.48 SEK | +262.31% | −93.80% | −94.62% |
| APTA.ST | Aptahem AB (publ) | 0.56 SEK | −15.96% | −51.69% | −67.65% |
| 0R55.L | BioSenic S.A. | 0.00 EUR | 0.00% | −4.76% | −25.93% |
| ALNEV.PA | Neovacs S.A. | 0.55 EUR | −31.22% | +6150.00% | −11.29% |
| 0A43.L | Inovio Pharmaceuticals, Inc. | $1.32 | +4.35% | −20.55% | −44.09% |
| 0A4D.L | Equillium, Inc. | $2.41 | +10.15% | +63.95% | +37.32% |
| 0A6I.L | Soligenix, Inc. | $0.39 | −4.04% | −71.78% | −87.16% |
| 0A8E.L | Xeris Biopharma Holdings, Inc. | $8.78 | +0.57% | +20.42% | +10.86% |
| 0A8U.L | Synlogic, Inc. | $1.23 | 0.00% | −1.17% | −15.17% |
| 0A9G.L | Mereo BioPharma Group plc | $0.28 | −2.36% | −42.56% | −84.25% |
| 0ABW.L | Egetis Therapeutics AB (publ) | 8.08 SEK | +8.09% | +63.15% | +58.43% |
| 0D1W.L | Biophytis S.A. | 0.07 EUR | −6.67% | +16.67% | −57.77% |
| 0JQ2.L | KALA BIO, Inc. | $0.82 | +0.07% | −97.18% | −99.84% |
| 0K1R.L | Viridian Therapeutics, Inc. | $24.40 | +1.29% | −21.12% | +30.27% |
| 0L49.L | SCYNEXIS, Inc. | $5.95 | +15.50% | +858.64% | +604.63% |
| 0QNS.L | Curatis Holding AG | 19.05 CHF | 0.00% | −15.71% | −15.71% |
| 0UNL.L | Nektar Therapeutics | $74.20 | +6.73% | +14.04% | +14.04% |
| 1AE.DE | argenx SE | 898.60 EUR | +15.89% | +24.05% | +38.37% |
| 2X1.DE | ABIVAX Société Anonyme | 100.50 EUR | −6.77% | −12.30% | +33.82% |
| BIOV.SW | BioVersys AG | 25.20 CHF | −6.67% | +6.33% | −9.03% |
| BPBS.PA | BIOPHYTIS BSA | 0.00 EUR | 0.00% | 0.00% | 0.00% |
| BSLN.SW | Basilea Pharmaceutica AG | 65.30 CHF | +24.62% | +19.82% | +40.88% |
| CESSA.CO | Cessatech A/S | 9.42 DKK | +9.53% | −48.38% | −48.38% |
| CURN.SW | Curatis Holding AG | 19.00 CHF | −11.21% | +45.59% | +65.22% |
| DBV.DE | DBV Technologies S.A. | 2.46 EUR | +12.83% | −25.17% | +64.35% |
| PHGN.DE | Pharming Group N.V. | 0.98 EUR | −10.95% | −32.74% | −21.41% |
| SANN.SW | Santhera Pharmaceuticals Holding AG | 15.70 CHF | +9.79% | +29.32% | +13.44% |
Covers ~22,000 companies across the US, Europe and Asia-Pacific (ex mainland China, Hong Kong and India), refreshed nightly. Every listed stock opens as a full analysis for $9.90.